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Familial Amyloid Neuropathies clinical trials in California

5 studies for Familial Amyloid Neuropathies are looking for participants at sites in California.

Cities in California

Non-interventional Study of Patients With Transthyretin (ATTR) Amyloidosis

  • Research Site, La Jolla
  • Research Site, Los Angeles
  • Research Site, San Francisco
  • and 1 more
RecruitingObservational study
Ages 18 to 130 · All sexes · Updated Sep 23, 2026 · NCT06465810

ConTTRibute: A Global Observational Study of Patients With Transthyretin (TTR)-Mediated Amyloidosis (ATTR Amyloidosis)

  • Clinical Trial Site, La Jolla
  • Clinical Trial Site, Los Angeles
RecruitingObservational study
All ages · All sexes · Updated Sep 8, 2026 · NCT04561518

Acoramidis Transthyretin Amyloidosis Prevention Trial in the Young (ACT-EARLY) Study in Asymptomatic Carriers of a Pathogenic TTR Variant

  • University of California, San Diego (UCSD) - Medical Center, La Jolla
  • University of California, Los Angeles (UCLA) - David Geffen School of Medicine, Los Angeles
  • University of California, San Francisco (UCSF), San Francisco
  • and 1 more
RecruitingPhase 3
Ages 18 to 75 · All sexes · Updated Aug 4, 2026 · NCT06563895

Artificial Intelligence Guided Echocardiographic Screening of Rare Diseases (EchoNet-Screening)

  • Cedars-Sinai Medical Centre (Los Angeles), Los Angeles
RecruitingObservational study
Ages 18 and older · All sexes · Updated Jul 22, 2026 · NCT05139797

Analysis of Lumbar Spine Stenosis Specimens for Identification of Transthyretin Cardiac Amyloidosis

  • Cedars-Sinai Medical Center, Beverly Hills
RecruitingObservational studyHealthy volunteers welcome
Ages 50 and older · All sexes · Updated Jun 4, 2026 · NCT06034405

From ClinicalTrials.gov, data retrieved Oct 6, 2026. Each study sets its own eligibility; the study team decides who can join.