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Mucopolysaccharidosis IV clinical trials in California
6 studies for Mucopolysaccharidosis IV are looking for participants at sites in California.
Prospective Clinical Assessment Study in Children With Hypochondroplasia
- UCSF Benioff Children's Hospital, Oakland
RecruitingObservational study
30 Months – 16 Years · All sexes · Updated Jul 16, 2026 · NCT06410976Interventional Study of Infigratinib in Children < 3 Years Old With Achondroplasia (ACH)
- UCSF Benioff Children's Hospital, Oakland
RecruitingPhase 2
0 Years – 32 Months · All sexes · Updated Jul 13, 2026 · NCT07169279A Study Evaluating the Impact of Regular FODMAP-targeting Digestive Enzyme Blend Use on Gastrointestinal Symptoms in Individuals With Self-Reported Bloating
- People Science, Los Angeles
RecruitingHealthy volunteers welcome
Ages 18 and older · All sexes · Updated May 15, 2026 · NCT07591584Registry of Patients Diagnosed With Lysosomal Storage Diseases
- University of California San Francisco, San Francisco
RecruitingObservational study
Up to age 64 · All sexes · Updated Apr 8, 2026 · NCT05619900PEARL (PrEnAtal Enzyme Replacement Therapy for Lysosomal Storage Disorders)
- University of California, San Francisco
RecruitingPhase 1
Ages 18 to 50 · Women · Updated Mar 17, 2026 · NCT04532047Cardiac Structure and Function in MPS
- Children'S Hospital of Orange County, Orange
RecruitingObservational studyHealthy volunteers welcome
Ages 0 to 99 · All sexes · Updated Jan 26, 2026 · NCT07361536From ClinicalTrials.gov, data retrieved Oct 5, 2026. Each study sets its own eligibility; the study team decides who can join.