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Fabry Disease clinical trials in California

3 studies for Fabry Disease are looking for participants at sites in California.

A Study to Learn How Well Lucerastat Works and How Safe it is in Untreated Adult Male Participants With Fabry Disease

  • UCSF Benioff Childens Hospital, Oakland
RecruitingPhase 3
Ages 18 to 60 · Men · Updated Nov 3, 2026 · NCT07778667

Fabry Disease Registry & Pregnancy Sub-registry

  • Southern California Permanente Medical Group- Site Number : 840108, Los Angeles
  • University Of California Los Angeles- Site Number : 840088, Los Angeles
  • Children's Hospital of Orange County- Site Number : 840074, Orange
  • and 4 more
RecruitingObservational study
All ages · All sexes · Updated Oct 14, 2026 · NCT00196742

Safety, PK/PD, and Exploratory Efficacy Study of AMT-191 in Classic Fabry Disease

  • University of California Los Angeles (UCLA), Los Angeles
RecruitingPhase 1/2
Ages 18 to 65 · Men · Updated Sep 24, 2026 · NCT06270316

From ClinicalTrials.gov, data retrieved Nov 15, 2026. Each study sets its own eligibility; the study team decides who can join.