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Genetic Disorders clinical trials in Missouri

4 studies for Genetic Disorders are looking for participants at sites in Missouri.

Cities in Missouri

Clinical and Genetic Evaluation of Individuals With Undiagnosed Disorders Through the Undiagnosed Diseases Network

  • Washington University in St. Louis, St Louis
RecruitingObservational studyHealthy volunteers welcome
1 Month – 100 Years · All sexes · Updated Nov 3, 2026 · NCT02450851

Study of Zodasiran in Adolescent Participants With Homozygous Familial Hypercholesterolemia

  • Research Site, St Louis
RecruitingPhase 3
Ages 12 to 17 · All sexes · Updated Oct 26, 2026 · NCT07473843

Prospective Clinical Assessment Study in Children With Hypochondroplasia

  • University of Missouri, Columbia
RecruitingObservational study
30 Months – 16 Years · All sexes · Updated Jul 16, 2026 · NCT06410976

Rett Syndrome Registry

  • Washington University in St. Louis, St Louis
RecruitingObservational study
Ages 0 to 99 · All sexes · Updated Jun 30, 2026 · NCT05432349

From ClinicalTrials.gov, data retrieved Nov 15, 2026. Each study sets its own eligibility; the study team decides who can join.