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Glycogen Storage Disease Type II clinical trials recruiting in the U.S.
10 studies for Glycogen Storage Disease Type II are recruiting participants at sites across the United States.
Cities with the most studies
- Durham, NC8 studies
- Arlington, VA5 studies
- St. Louis, MO5 studies
- Irvine, CA5 studies
- Atlanta, GA4 studies
- New York City, NY4 studies
- Pittsburgh, PA4 studies
- Philadelphia, PA4 studies
- Jacksonville, FL3 studies
- Indianapolis, IN3 studies
- Phoenix, AZ3 studies
- Cincinnati, OH3 studies
By state
- Arizona3 studies
- California5 studies
- Florida4 studies
- Georgia4 studies
- Indiana3 studies
- Missouri6 studies
- New York4 studies
- North Carolina8 studies
- Ohio4 studies
- Pennsylvania4 studies
- Virginia6 studies
Recently updated studies
A Study to Evaluate the Safety, Pharmacokinetics, and Pharmacodynamics of DNL952 in Adult Participants With Late-Onset Pompe Disease
RecruitingPhase 1
Ages 18 to 75 · All sexes · Updated Aug 17, 2026 · NCT07354724A Study to Evaluate Safety, Tolerability, and Efficacy of AB-1009 Gene Therapy (GAA Gene) in Adult Participants With Late-Onset Pompe Disease (PROGRESS-GT LOPD)
RecruitingPhase 1/2
Ages 18 to 65 · All sexes · Updated Jul 20, 2026 · NCT07282847Pompe Disease Registry Protocol
RecruitingObservational study
All ages · All sexes · Updated Jun 23, 2026 · NCT00231400Study of S-606001 as an Add-on to Enzyme Replacement Therapy (ERT) in Participants With Late-onset Pompe Disease (LOPD)
RecruitingPhase 2
Ages 18 and older · All sexes · Updated Jun 23, 2026 · NCT07123155Pompe Pregnancy Sub-Registry
RecruitingObservational study
All ages · Women · Updated Apr 16, 2026 · NCT00567073Determination of CRIM Status and Longitudinal Follow-up of Individuals With Pompe Disease
RecruitingObservational study
All ages · All sexes · Updated Apr 8, 2026 · NCT01665326Effects of Whole-body Electrical Muscle Stimulation Exercise on Adults With Neuromuscular Disease
Recruiting
Ages 18 and older · All sexes · Updated Mar 17, 2026 · NCT07478172A Global Prospective Observational Registry of Patients With Pompe Disease
RecruitingObservational study
All ages · All sexes · Updated Mar 10, 2026 · NCT06121011Cognitive and Neurological Pathologies in Pompe Disease
RecruitingObservational study
Ages 0 to 18 · All sexes · Updated Mar 4, 2026 · NCT04639336Avalglucosidase Alfa Pregnancy Study
RecruitingObservational study
All ages · Women · Updated Jan 16, 2026 · NCT05734521From ClinicalTrials.gov, data retrieved Oct 5, 2026. Each study sets its own eligibility; the study team decides who can join.