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Inborn Errors Metabolism clinical trials in California
6 studies for Inborn Errors Metabolism are looking for participants at sites in California.
Cities in California
A Long-Term Observational Study of Patients With Fucosidosis
- Children's Hospital of Orange County, Orange
RecruitingObservational study
All ages · All sexes · Updated Sep 17, 2026 · NCT07615400An Open-label Study to Investigate ECUR-506 in Male Babies Less Than 9 Months of Age With Neonatal Onset OTC Deficiency
- UCLA Mattel Children's Hospital, Los Angeles
RecruitingPhase 3
24 Hours – 7 Months · Men · Updated Aug 12, 2026 · NCT06255782Registry of Patients Diagnosed With Lysosomal Storage Diseases
- University of California San Francisco, San Francisco
RecruitingObservational study
Up to age 64 · All sexes · Updated Apr 8, 2026 · NCT05619900A Study to Assess the Long-term Safety and Clinical Activity of mRNA-3927 in Participants Previously Enrolled in the mRNA-3927-P101 Study
- Ronald Reagan UCLA Medical Center, Los Angeles
- University of Stanford Medical Center, Palo Alto
RecruitingPhase 1/2
Ages 1 and older · All sexes · Updated Mar 23, 2026 · NCT05130437Open-Label Study of mRNA-3927 in Participants With Propionic Acidemia
- UCSD Altman Clinical and Transalational Research Institute Building, Los Angeles
- Ronald Reagan UCLA Medical Center, Los Angeles
- Lucile Packard Children's Hospital Stanford, Stanford
RecruitingPhase 1/2
All ages · All sexes · Updated Jan 22, 2026 · NCT04159103An Extension Study to Evaluate the Long-Term Safety and Clinical Activity of mRNA-3705 in Participants Previously Enrolled in Other Clinical Studies of mRNA-3705
- UCLA Medical Center, Los Angeles
- Lucile Packard Children's Hospital at Stanford, Palo Alto
- Altman Clinical and Translational Research Institution, San Diego
RecruitingPhase 1/2
Ages 1 and older · All sexes · Updated Dec 23, 2025 · NCT05295433From ClinicalTrials.gov, data retrieved Sep 30, 2026. Each study sets its own eligibility; the study team decides who can join.