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Inborn Errors Metabolism clinical trials in Pennsylvania
6 studies for Inborn Errors Metabolism are looking for participants at sites in Pennsylvania.
Cities in Pennsylvania
Natural History, Physiology, Microbiome and Biochemistry Studies of Propionic Acidemia
- Children's Hospital of Pittsburgh, Pittsburgh
RecruitingObservational studyHealthy volunteers welcome
1 Month – 100 Years · All sexes · Updated Sep 28, 2026 · NCT02890342Clinical and Laboratory Study of Methylmalonic Acidemia
- UPMC Children's Hospital of Pittsburgh, Pittsburgh
RecruitingObservational studyHealthy volunteers welcome
1 Month – 115 Years · All sexes · Updated Sep 10, 2026 · NCT00078078Phase 1/2: CD45RA Depleted Stem Cell Addback to Prevent Viral or Fungal Infections Post TCRab/CD19 Depleted HSCT
- Children's Hospital of Philadelphia, Philadelphia
RecruitingPhase 1/2
1 Month – 25 Years · All sexes · Updated Apr 15, 2026 · NCT06839456A Study to Assess the Long-term Safety and Clinical Activity of mRNA-3927 in Participants Previously Enrolled in the mRNA-3927-P101 Study
- The Children's Hospital of Philadelphia (CHOP), Philadelphia
RecruitingPhase 1/2
Ages 1 and older · All sexes · Updated Mar 23, 2026 · NCT05130437Expanded Access Protocol Using CD3+/CD19+ Depleted PBSC
- Children's Hospital of Philadelphia, Philadelphia
RecruitingEarly phase 1
Up to age 30 · All sexes · Updated Feb 20, 2026 · NCT02356653Open-Label Study of mRNA-3927 in Participants With Propionic Acidemia
- Children's Hospital of Philadelphia (CHOP), Philadelphia
RecruitingPhase 1/2
All ages · All sexes · Updated Jan 22, 2026 · NCT04159103From ClinicalTrials.gov, data retrieved Sep 30, 2026. Each study sets its own eligibility; the study team decides who can join.