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Leukodystrophies clinical trials in Pennsylvania
4 studies for Leukodystrophies are looking for participants at sites in Pennsylvania.
Cities in Pennsylvania
Longitudinal Study of Neurodegenerative Disorders
- UPMC Children's Hospital of Pittsburgh, Pittsburgh
RecruitingObservational study
All ages · All sexes · Updated Feb 9, 2026 · NCT03333200Data Collection Study of Patients With Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT With RIC
- UPMC Children's Hospital of Pittsburgh, Pittsburgh
RecruitingObservational study
2 Months – 60 Years · All sexes · Updated Jan 13, 2026 · NCT04528355Reduced Intensity Conditioning for Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT
- UPMC Children's Hospital of Pittsburgh, Pittsburgh
RecruitingPhase 2
2 Months – 55 Years · All sexes · Updated Dec 15, 2025 · NCT01962415The Myelin Disorders Biorepository Project
- The Children's Hospital of Philadelphia, Philadelphia
- University of Pennsylvania, Philadelphia
- University of Pittsburgh Medical Center, Pittsburgh
RecruitingObservational study
All ages · All sexes · Updated Oct 23, 2025 · NCT03047369From ClinicalTrials.gov, data retrieved Oct 1, 2026. Each study sets its own eligibility; the study team decides who can join.