🔎 Trials Near Me

Home › Paroxysmal Hemoglobinuria

Paroxysmal Hemoglobinuria clinical trials recruiting in the U.S.

9 studies for Paroxysmal Hemoglobinuria are recruiting participants at sites across the United States.

Cities with the most studies

By state

Recently updated studies

Study to Assess the Pharmacokinetics, Safety, and Tolerability of Iptacopan in Pediatric PNH Patients

RecruitingPhase 3
Ages 2 to 18 · All sexes · Updated Aug 7, 2026 · NCT06934967

A Study of Pegcetacoplan in Pediatric Patients With Paroxysmal Nocturnal Hemoglobinuria (PNH)

RecruitingPhase 2
Ages 12 to 17 · All sexes · Updated Jun 26, 2026 · NCT04901936

Study of Ultomiris® (Ravulizumab) Safety in Pregnancy

RecruitingObservational study
All ages · Women · Updated Apr 16, 2026 · NCT06312644

Home Reported Outcomes in PNH

RecruitingObservational study
Ages 18 to 99 · All sexes · Updated Aug 27, 2025 · NCT06411626

Global PNH Patient Registry

RecruitingObservational study
All ages · All sexes · Updated Feb 20, 2025 · NCT05755867

The International PNH Interest Group PNH Registry

RecruitingObservational study
All ages · All sexes · Updated Jul 29, 2024 · NCT06524726

From ClinicalTrials.gov, data retrieved Oct 2, 2026. Each study sets its own eligibility; the study team decides who can join.