Home › Rare Diseases › Missouri
Rare Diseases clinical trials in Missouri
4 studies for Rare Diseases are looking for participants at sites in Missouri.
Cities in Missouri
Clinical and Genetic Evaluation of Individuals With Undiagnosed Disorders Through the Undiagnosed Diseases Network
- Washington University in St. Louis, St Louis
RecruitingObservational studyHealthy volunteers welcome
1 Month – 100 Years · All sexes · Updated Oct 2, 2026 · NCT02450851Study of S-606001 as an Add-on to Enzyme Replacement Therapy (ERT) in Participants With Late-onset Pompe Disease (LOPD)
- Washington University in St. Louis, St Louis
RecruitingPhase 2
Ages 18 and older · All sexes · Updated Jun 23, 2026 · NCT07123155Baker Gordon Syndrome Natural History Study
- University of Missouri Columbia, Columbia
RecruitingObservational study
Ages 0 to 99 · All sexes · Updated Jun 3, 2026 · NCT06399952The ExTINGUISH Trial of Inebilizumab in NMDAR Encephalitis
- Washington University in St. Louis School of Medicine, St Louis
RecruitingPhase 2
Ages 12 and older · All sexes · Updated Jul 1, 2025 · NCT04372615From ClinicalTrials.gov, data retrieved Oct 5, 2026. Each study sets its own eligibility; the study team decides who can join.