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Rett Syndrome clinical trials in California

4 studies for Rett Syndrome are looking for participants at sites in California.

Cities in California

Rett Syndrome Registry

  • Children's Hospital Los Angeles, Los Angeles
  • UCSF Benioff Children's Hospital, Oakland
  • Rady Children's Hospital - San Diego, San Diego
RecruitingObservational study
Ages 0 to 99 · All sexes · Updated Jun 30, 2026 · NCT05432349

To Investigate the Efficacy of Treatment With Oral NA-921 (Bionetide) Versus Placebo in Females With Rett Syndrome

  • Biomed Testing Facility # BIO-05-92093, La Jolla
  • Biomed Testing Facility # BIO-04-90095, Los Angeles
  • Biomed Testing Facility # BIO-03-95817, Sacramento
  • and 1 more
RecruitingPhase 3
Ages 5 to 20 · Women · Updated Mar 27, 2026 · NCT06840496

Neurophysiologic Biomarkers in Rett Syndrome

  • Children's Hospital of Los Angeles, Los Angeles
RecruitingObservational studyHealthy volunteers welcome
Ages 1 to 18 · Women · Updated Oct 20, 2025 · NCT05932589

From ClinicalTrials.gov, data retrieved Oct 1, 2026. Each study sets its own eligibility; the study team decides who can join.