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Rett Syndrome clinical trials in Florida

3 studies for Rett Syndrome are looking for participants at sites in Florida.

A Phase 3 Study of Fenfluramine Hydrochloride in Rett Syndrome

  • Ep0247 21009, Miami
  • Ep0247 21011, Orlando
RecruitingPhase 3
Ages 5 to 35 · All sexes · Updated Sep 18, 2026 · NCT07503444

Rett Syndrome Registry

  • Nicklaus Children's Hospital, Miami
RecruitingObservational study
Ages 0 to 99 · All sexes · Updated Jun 30, 2026 · NCT05432349

To Investigate the Efficacy of Treatment With Oral NA-921 (Bionetide) Versus Placebo in Females With Rett Syndrome

  • Biomed Testing Facility #BIO-07-33606, Tampa
RecruitingPhase 3
Ages 5 to 20 · Women · Updated Mar 27, 2026 · NCT06840496

From ClinicalTrials.gov, data retrieved Sep 30, 2026. Each study sets its own eligibility; the study team decides who can join.