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Severe Combined Immunodeficiency clinical trials recruiting in the U.S.
5 studies for Severe Combined Immunodeficiency are recruiting participants at sites across the United States.
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Recently updated studies
Genetic Basis of Immunodeficiency
RecruitingObservational study
6 Months – 99 Years · All sexes · Updated Sep 28, 2026 · NCT00055172Hematopoietic Stem Cell Transplantation (HSCT) for Common Variable Immunodeficiency (CVID) and Other Autoimmune Manifestations of Primary Immune Regulatory Disorders (PIRD)
RecruitingPhase 2
Ages 5 to 40 · All sexes · Updated May 15, 2026 · NCT07284641Autologous Gene Therapy for Artemis-Deficient SCID
RecruitingPhase 1/2
2 Months · All sexes · Updated Feb 13, 2026 · NCT03538899Data Collection Study of Patients With Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT With RIC
RecruitingObservational study
2 Months – 60 Years · All sexes · Updated Jan 13, 2026 · NCT04528355Reduced Intensity Conditioning for Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT
RecruitingPhase 2
2 Months – 55 Years · All sexes · Updated Dec 15, 2025 · NCT01962415From ClinicalTrials.gov, data retrieved Oct 1, 2026. Each study sets its own eligibility; the study team decides who can join.