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Transthyretin-Related Hereditary Amyloidosis clinical trials in Pennsylvania

4 studies for Transthyretin-Related Hereditary Amyloidosis are looking for participants at sites in Pennsylvania.

Cities in Pennsylvania

Non-interventional Study of Patients With Transthyretin (ATTR) Amyloidosis

  • Research Site, Danville
  • Research Site, Philadelphia
  • Research Site, Philadelphia
RecruitingObservational study
Ages 18 to 130 · All sexes · Updated Sep 23, 2026 · NCT06465810

ConTTRibute: A Global Observational Study of Patients With Transthyretin (TTR)-Mediated Amyloidosis (ATTR Amyloidosis)

  • Clinical Trial Site, Philadelphia
RecruitingObservational study
All ages · All sexes · Updated Sep 8, 2026 · NCT04561518

Acoramidis Transthyretin Amyloidosis Prevention Trial in the Young (ACT-EARLY) Study in Asymptomatic Carriers of a Pathogenic TTR Variant

  • Penn Presbyterian Medical Center, Philadelphia
  • University of Pittsburgh Medical Center, Presbyterian Hospital, Pittsburgh
RecruitingPhase 3
Ages 18 to 75 · All sexes · Updated Aug 4, 2026 · NCT06563895

MAGNITUDE: A Phase 3 Study of NTLA-2001 in Participants With Transthyretin Amyloidosis With Cardiomyopathy (ATTR-CM)

  • Penn Presbyterian Medical Center, Philadelphia
  • Allegheny General Hospital, Pittsburgh
  • University of Pittsburgh Medical Center, Pittsburgh
RecruitingPhase 3
Ages 18 to 90 · All sexes · Updated Mar 27, 2026 · NCT06128629

From ClinicalTrials.gov, data retrieved Oct 6, 2026. Each study sets its own eligibility; the study team decides who can join.