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X-Linked Genetic Diseases clinical trials in Colorado
3 studies for X-Linked Genetic Diseases are looking for participants at sites in Colorado.
Long-term Follow-up (LTFU) Study of Participants in Any iECURE Protocol Using an Investigational Product (IP)
- Children's Hospital of Colorado, Anshutz Medical Campus, Aurora
RecruitingObservational study
7 Months – 15 Months · All sexes · Updated Aug 31, 2026 · NCT06805695Rett Syndrome Registry
- Children's Hospital Colorado, Denver
RecruitingObservational study
Ages 0 to 99 · All sexes · Updated Jun 30, 2026 · NCT05432349To Investigate the Efficacy of Treatment With Oral NA-921 (Bionetide) Versus Placebo in Females With Rett Syndrome
- Biomed Testing Facility #BIO-06-80042, Aurora
RecruitingPhase 3
Ages 5 to 20 · Women · Updated Mar 27, 2026 · NCT06840496From ClinicalTrials.gov, data retrieved Oct 1, 2026. Each study sets its own eligibility; the study team decides who can join.