Hjem › Adrenoleukodystrofi › Pennsylvania
Adrenoleukodystrofi kliniske forsøg i Pennsylvania
4 studier for Adrenoleukodystrofi søger deltagere på steder i Pennsylvania.
Byer i Pennsylvania
Officiel studietekst (engelsk)
Data Collection Study of Patients With Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT With RIC
- UPMC Children's Hospital of Pittsburgh, Pittsburgh
RekruttererObservationsstudie
2 Months – 60 Years · Alle køn · Opdateret 13. jan. 2026 · NCT04528355Reduced Intensity Conditioning for Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT
- UPMC Children's Hospital of Pittsburgh, Pittsburgh
RekruttererFase 2
2 Months – 55 Years · Alle køn · Opdateret 15. dec. 2025 · NCT01962415The Myelin Disorders Biorepository Project
- The Children's Hospital of Philadelphia, Philadelphia
- University of Pennsylvania, Philadelphia
- University of Pittsburgh Medical Center, Pittsburgh
RekruttererObservationsstudie
Alle aldre · Alle køn · Opdateret 23. okt. 2025 · NCT03047369A Study of Participants With Cerebral Adrenoleukodystrophy (CALD) Treated With Elivaldogene Autotemcel
- Children's Hospital of Philadelphia, Philadelphia
RekruttererObservationsstudie
Alle aldre · Mænd · Opdateret 2. jul. 2025 · NCT06224413Fra ClinicalTrials.gov, data hentet 4. okt. 2026. Hver studie har sine egne kvalifikationskrav; studieteamet afgør, hvem der kan deltage.