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Adrenoleukodystrofi kliniske forsøg i Pennsylvania

4 studier for Adrenoleukodystrofi søger deltagere på steder i Pennsylvania.

Byer i Pennsylvania

Officiel studietekst (engelsk)

Data Collection Study of Patients With Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT With RIC

  • UPMC Children's Hospital of Pittsburgh, Pittsburgh
RekruttererObservationsstudie
2 Months – 60 Years · Alle køn · Opdateret 13. jan. 2026 · NCT04528355

Reduced Intensity Conditioning for Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT

  • UPMC Children's Hospital of Pittsburgh, Pittsburgh
RekruttererFase 2
2 Months – 55 Years · Alle køn · Opdateret 15. dec. 2025 · NCT01962415

The Myelin Disorders Biorepository Project

  • The Children's Hospital of Philadelphia, Philadelphia
  • University of Pennsylvania, Philadelphia
  • University of Pittsburgh Medical Center, Pittsburgh
RekruttererObservationsstudie
Alle aldre · Alle køn · Opdateret 23. okt. 2025 · NCT03047369

A Study of Participants With Cerebral Adrenoleukodystrophy (CALD) Treated With Elivaldogene Autotemcel

  • Children's Hospital of Philadelphia, Philadelphia
RekruttererObservationsstudie
Alle aldre · Mænd · Opdateret 2. jul. 2025 · NCT06224413

Fra ClinicalTrials.gov, data hentet 4. okt. 2026. Hver studie har sine egne kvalifikationskrav; studieteamet afgør, hvem der kan deltage.