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Amyloidose kliniske forsøg i Pennsylvania

7 studier for Amyloidose søger deltagere på steder i Pennsylvania.

Byer i Pennsylvania

Officiel studietekst (engelsk)

A Study of JNJ-79635322 in Participants With Relapsed or Refractory Multiple Myeloma or Previously Treated Amyloid Light-chain (AL) Amyloidosis

  • University of Pennsylvania Division of Hematology Oncology Perelman Center for Advanced Medicine, Philadelphia
RekruttererFase 1
Alder 18 og opefter · Alle køn · Opdateret 28. sep. 2026 · NCT05652335

Non-interventional Study of Patients With Transthyretin (ATTR) Amyloidosis

  • Research Site, Danville
  • Research Site, Philadelphia
  • Research Site, Philadelphia
RekruttererObservationsstudie
Alder 18 til 130 · Alle køn · Opdateret 23. sep. 2026 · NCT06465810

TRITON-CM: A Study to Evaluate Nucresiran in Patients With Transthyretin Amyloidosis With Cardiomyopathy

  • Clinical Trial Site, Lancaster
  • Clinical Trial Site, Philadelphia
RekruttererFase 3
Alder 18 til 85 · Alle køn · Opdateret 16. sep. 2026 · NCT07052903

DemonsTTRate: A Global, Observational, Multicenter, Long-term Study of Patients With ATTR-CM in a Real-World Setting

  • Clinical Trial Site, Philadelphia
RekruttererObservationsstudie
Alder 18 og opefter · Alle køn · Opdateret 9. sep. 2026 · NCT07358078

ConTTRibute: A Global Observational Study of Patients With Transthyretin (TTR)-Mediated Amyloidosis (ATTR Amyloidosis)

  • Clinical Trial Site, Philadelphia
RekruttererObservationsstudie
Alle aldre · Alle køn · Opdateret 8. sep. 2026 · NCT04561518

Acoramidis Transthyretin Amyloidosis Prevention Trial in the Young (ACT-EARLY) Study in Asymptomatic Carriers of a Pathogenic TTR Variant

  • Penn Presbyterian Medical Center, Philadelphia
  • University of Pittsburgh Medical Center, Presbyterian Hospital, Pittsburgh
RekruttererFase 3
Alder 18 til 75 · Alle køn · Opdateret 4. aug. 2026 · NCT06563895

MAGNITUDE: A Phase 3 Study of NTLA-2001 in Participants With Transthyretin Amyloidosis With Cardiomyopathy (ATTR-CM)

  • Penn Presbyterian Medical Center, Philadelphia
  • Allegheny General Hospital, Pittsburgh
  • University of Pittsburgh Medical Center, Pittsburgh
RekruttererFase 3
Alder 18 til 90 · Alle køn · Opdateret 27. mar. 2026 · NCT06128629

Fra ClinicalTrials.gov, data hentet 5. okt. 2026. Hver studie har sine egne kvalifikationskrav; studieteamet afgør, hvem der kan deltage.