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Beta-thalassæmi kliniske forsøg i Pennsylvania

5 studier for Beta-thalassæmi søger deltagere på steder i Pennsylvania.

Byer i Pennsylvania

Officiel studietekst (engelsk)

ALS20-101 Lentiviral Gene Therapy for Beta Thalassemia

  • Children's Hospital of Philadelphia, Philadelphia
RekruttererFase 1/2
Alder 18 til 40 · Alle køn · Opdateret 23. sep. 2026 · NCT06364774

T-Cell Depleted Alternative Donor Bone Marrow Transplant for Sickle Cell Disease (SCD) and Other Anemias

  • Children's Hospital of Pittsburgh of UPMC, Pittsburgh
RekruttererFase 1/2
Alder 5 til 40 · Alle køn · Opdateret 13. aug. 2026 · NCT03653338

Data Collection Study of Patients With Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT With RIC

  • UPMC Children's Hospital of Pittsburgh, Pittsburgh
RekruttererObservationsstudie
2 Months – 60 Years · Alle køn · Opdateret 13. jan. 2026 · NCT04528355

Reduced Intensity Conditioning for Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT

  • UPMC Children's Hospital of Pittsburgh, Pittsburgh
RekruttererFase 2
2 Months – 55 Years · Alle køn · Opdateret 15. dec. 2025 · NCT01962415

A Study of Participants with Β-Thalassemia Treated with Betibeglogene Autotemcel

  • Children's Hospital of Philadelphia, Philadelphia
RekruttererObservationsstudie
Alle aldre · Alle køn · Opdateret 11. feb. 2025 · NCT06271512

Fra ClinicalTrials.gov, data hentet 5. okt. 2026. Hver studie har sine egne kvalifikationskrav; studieteamet afgør, hvem der kan deltage.