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Duchennes muskeldystrofi kliniske forsøg i Virginia
4 studier for Duchennes muskeldystrofi søger deltagere på steder i Virginia.
Byer i Virginia
Officiel studietekst (engelsk)
A Study of SGT-003 Gene Therapy in Ambulant Males With Duchenne Muscular Dystrophy (IMPACT DUCHENNE)
- Children's Hospital of the King's Daughters, Norfolk
RekruttererFase 3
Alder 7 til 11 · Mænd · Opdateret 28. sep. 2026 · NCT07160634A Gene Transfer Therapy Study to Evaluate the Safety of and Expression From Delandistrogene Moxeparvovec (SRP-9001) in Participants With Duchenne Muscular Dystrophy (DMD) - Non-Ambulatory Cohort
- Children's Hospital of The King's Daughters, Norfolk
RekruttererFase 1
Alder 2 og opefter · Mænd · Opdateret 11. sep. 2026 · NCT04626674Modeling Mortality in Duchenne Muscular Dystrophy Cardiomyopathy: Identification of Surrogate Outcome Measures for DMD Drug Trials
- Children's Hospital of Richmond at VCU, Richmond
RekruttererObservationsstudie
Alle aldre · Alle køn · Opdateret 28. jul. 2026 · NCT07674758A Study of SGT-003 Gene Therapy in Duchenne Muscular Dystrophy (INSPIRE DUCHENNE)
- Children's Hospital of the King's Daughters, Norfolk
RekruttererFase 1/2
Alder 0 til 17 · Mænd · Opdateret 8. jul. 2026 · NCT06138639Fra ClinicalTrials.gov, data hentet 5. okt. 2026. Hver studie har sine egne kvalifikationskrav; studieteamet afgør, hvem der kan deltage.