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Fabrys sygdom kliniske forsøg i Minnesota

4 studier for Fabrys sygdom søger deltagere på steder i Minnesota.

Byer i Minnesota

Officiel studietekst (engelsk)

Safety, PK/PD, and Exploratory Efficacy Study of AMT-191 in Classic Fabry Disease

  • MHealth Fairview University of Minnesota Medical Center East Bank, Minneapolis
RekruttererFase 1/2
Alder 18 til 65 · Mænd · Opdateret 24. sep. 2026 · NCT06270316

A Study of Migalastat in Pediatric Subjects (2 to <12 Yrs) With Fabry Disease and Amenable GLA Variants

  • University of Minnesota Masonic Children's Hospital, Minneapolis
RekruttererFase 3
Alder 2 til 11 · Alle køn · Opdateret 1. sep. 2026 · NCT06904261

Natural History and Structural Functional Relationships in Fabry Renal Disease Treatment Outcomes(Changes)in Fabry Renal Disease Study

  • University of Minnesota, Minneapolis
  • Universtity of Minnesota, Department of Pediatric Nephrology, Minneapolis
RekruttererObservationsstudie
Alder 1 til 75 · Alle køn · Opdateret 14. aug. 2026 · NCT01581424

Fabry Disease Registry & Pregnancy Sub-registry

  • Children's Hospitals and Clinics of Minnesota- Site Number : 840114, Minneapolis
  • M Health Fairview University of Minnesota Medical Center - West Bank- Site Number : 840076, Minneapolis
RekruttererObservationsstudie
Alle aldre · Alle køn · Opdateret 23. jun. 2026 · NCT00196742

Fra ClinicalTrials.gov, data hentet 4. okt. 2026. Hver studie har sine egne kvalifikationskrav; studieteamet afgør, hvem der kan deltage.