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Fabrys sygdom kliniske forsøg i Pennsylvania

5 studier for Fabrys sygdom søger deltagere på steder i Pennsylvania.

Byer i Pennsylvania

Officiel studietekst (engelsk)

Safety, PK/PD, and Exploratory Efficacy Study of AMT-191 in Classic Fabry Disease

  • UPMC Children's Hospital of Pittsburgh, Pittsburgh
RekruttererFase 1/2
Alder 18 til 65 · Mænd · Opdateret 24. sep. 2026 · NCT06270316

A Study of Patients With Fabry Disease (US Specific)

  • UPMC Children's Hospital of Pittsburgh, Pittsburgh
RekruttererObservationsstudie
Alder 18 og opefter · Alle køn · Opdateret 9. sep. 2026 · NCT06906367

A Study of Migalastat in Pediatric Subjects (2 to <12 Yrs) With Fabry Disease and Amenable GLA Variants

  • UPMC Children's Hospital of Pittsburgh, Pittsburgh
RekruttererFase 3
Alder 2 til 11 · Alle køn · Opdateret 1. sep. 2026 · NCT06904261

Fabry Disease Registry & Pregnancy Sub-registry

  • Geisinger Medical Center- Site Number : 840111, Danville
  • Penn State University Medical Center-Neurology- Site Number : 840104, Hershey
  • Children's Hospital of Philadelphia HUP Medical Genetics- Site Number : 840089, Philadelphia
  • og 2 flere
RekruttererObservationsstudie
Alle aldre · Alle køn · Opdateret 23. jun. 2026 · NCT00196742

A Global Prospective Observational Study of Women With Fabry Disease and Their Infants During Pregnancy and Breastfeeding

  • Amicus Therapeutics, Inc. Pregnancy Registry, Philadelphia
RekruttererObservationsstudie
Alle aldre · Kvinder · Opdateret 8. jul. 2025 · NCT04252066

Fra ClinicalTrials.gov, data hentet 5. okt. 2026. Hver studie har sine egne kvalifikationskrav; studieteamet afgør, hvem der kan deltage.