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Gauchers sygdom kliniske forsøg i Pennsylvania

5 studier for Gauchers sygdom søger deltagere på steder i Pennsylvania.

Byer i Pennsylvania

Officiel studietekst (engelsk)

A Gaucher Disease Gene Therapy Trial With FLT201

  • Children's Hospital of Philadelphia, Philadelphia
  • UPMC Children's Hospital of Pittsburgh, Pittsburgh
RekruttererFase 3
Alder 18 og opefter · Alle køn · Opdateret 3. sep. 2026 · NCT07223944

International Collaborative Gaucher Group (ICGG) Gaucher Disease Registry & Pregnancy Sub-registry

  • Penn State Health Milton South Hershey Medical Center- Site Number : 840126, Hershey
  • Children's Hospital of Philadelphia HUP Medical Genetics- Site Number : 840089, Philadelphia
  • Children's Hospital of Philadelphia- Site Number : 840034, Philadelphia
  • og 1 flere
RekruttererObservationsstudie
Alle aldre · Alle køn · Opdateret 14. apr. 2026 · NCT00358943

Longitudinal Study of Neurodegenerative Disorders

  • UPMC Children's Hospital of Pittsburgh, Pittsburgh
RekruttererObservationsstudie
Alle aldre · Alle køn · Opdateret 9. feb. 2026 · NCT03333200

Data Collection Study of Patients With Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT With RIC

  • UPMC Children's Hospital of Pittsburgh, Pittsburgh
RekruttererObservationsstudie
2 Months – 60 Years · Alle køn · Opdateret 13. jan. 2026 · NCT04528355

Reduced Intensity Conditioning for Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT

  • UPMC Children's Hospital of Pittsburgh, Pittsburgh
RekruttererFase 2
2 Months – 55 Years · Alle køn · Opdateret 15. dec. 2025 · NCT01962415

Fra ClinicalTrials.gov, data hentet 5. okt. 2026. Hver studie har sine egne kvalifikationskrav; studieteamet afgør, hvem der kan deltage.