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Glykogengemmelsessygdom type II kliniske forsøg i Missouri

6 studier for Glykogengemmelsessygdom type II søger deltagere på steder i Missouri.

Byer i Missouri

Officiel studietekst (engelsk)

A Study to Evaluate the Safety, Pharmacokinetics, and Pharmacodynamics of DNL952 in Adult Participants With Late-Onset Pompe Disease

  • Washington University School of Medicine, St Louis
RekruttererFase 1
Alder 18 til 75 · Alle køn · Opdateret 17. aug. 2026 · NCT07354724

Pompe Disease Registry Protocol

  • University of Missouri Health System Department of Genetics- Site Number : 840031, Columbia
  • Washington University- Site Number : 840100, St Louis
RekruttererObservationsstudie
Alle aldre · Alle køn · Opdateret 23. jun. 2026 · NCT00231400

Study of S-606001 as an Add-on to Enzyme Replacement Therapy (ERT) in Participants With Late-onset Pompe Disease (LOPD)

  • Washington University in St. Louis, St Louis
RekruttererFase 2
Alder 18 og opefter · Alle køn · Opdateret 23. jun. 2026 · NCT07123155

Pompe Pregnancy Sub-Registry

  • Washington University- Site Number : 150612, St Louis
RekruttererObservationsstudie
Alle aldre · Kvinder · Opdateret 16. apr. 2026 · NCT00567073

Effects of Whole-body Electrical Muscle Stimulation Exercise on Adults With Neuromuscular Disease

  • NextGen Precision Health Building, Clinical and Translational Science Unit, Columbia
Rekrutterer
Alder 18 og opefter · Alle køn · Opdateret 17. mar. 2026 · NCT07478172

A Global Prospective Observational Registry of Patients With Pompe Disease

  • Washington University School of Medicine, St Louis
RekruttererObservationsstudie
Alle aldre · Alle køn · Opdateret 10. mar. 2026 · NCT06121011

Fra ClinicalTrials.gov, data hentet 5. okt. 2026. Hver studie har sine egne kvalifikationskrav; studieteamet afgør, hvem der kan deltage.