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Glykogengemmelsessygdom type II kliniske forsøg i Virginia

6 studier for Glykogengemmelsessygdom type II søger deltagere på steder i Virginia.

Byer i Virginia

Officiel studietekst (engelsk)

A Study to Evaluate the Safety, Pharmacokinetics, and Pharmacodynamics of DNL952 in Adult Participants With Late-Onset Pompe Disease

  • The Lysosomal & Rare Disorders Research & Treatment Center, Fairfax
RekruttererFase 1
Alder 18 til 75 · Alle køn · Opdateret 17. aug. 2026 · NCT07354724

A Study to Evaluate Safety, Tolerability, and Efficacy of AB-1009 Gene Therapy (GAA Gene) in Adult Participants With Late-Onset Pompe Disease (PROGRESS-GT LOPD)

  • Virginia Commonwealth University (VCU), Richmond
RekruttererFase 1/2
Alder 18 til 65 · Alle køn · Opdateret 20. jul. 2026 · NCT07282847

Pompe Disease Registry Protocol

  • O & O Alpan- Site Number : 840025, Fairfax
RekruttererObservationsstudie
Alle aldre · Alle køn · Opdateret 23. jun. 2026 · NCT00231400

Study of S-606001 as an Add-on to Enzyme Replacement Therapy (ERT) in Participants With Late-onset Pompe Disease (LOPD)

  • Lysosomal and Rare Disorders Research and Treatment Center (LDRTC), Fairfax
RekruttererFase 2
Alder 18 og opefter · Alle køn · Opdateret 23. jun. 2026 · NCT07123155

Pompe Pregnancy Sub-Registry

  • O & O Alpan- Site Number : 840025, Fairfax
RekruttererObservationsstudie
Alle aldre · Kvinder · Opdateret 16. apr. 2026 · NCT00567073

A Global Prospective Observational Registry of Patients With Pompe Disease

  • Lysosomal and Rare Disorders Research and Treatment Center, Inc., Fairfax
RekruttererObservationsstudie
Alle aldre · Alle køn · Opdateret 10. mar. 2026 · NCT06121011

Fra ClinicalTrials.gov, data hentet 5. okt. 2026. Hver studie har sine egne kvalifikationskrav; studieteamet afgør, hvem der kan deltage.