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Hæmofili B kliniske forsøg i Californien

7 studier for Hæmofili B søger deltagere på steder i Californien.

Byer i Californien

Officiel studietekst (engelsk)

Safety and Effectiveness of Giroctocogene Fitelparvovec or Fidanacogene Elaparvovec in Patients With Hemophilia A or B Respectively

  • The Regents of the University of California||UC Davis Health, Rancho Cordova
  • UC Davis Health, Sacramento
  • UC Davis Ambulatory Care Clinic, Sacramento
  • og 3 flere
RekruttererFase 3
Alder 18 og opefter · Mænd · Opdateret 2. okt. 2026 · NCT05568719

Phase 3, Open-label, Single-dose Study of CSL222 in Adolescent Male Subjects (≥ 12 to < 18 Years of Age) With Severe or Moderately Severe Hemophilia B

  • Center for Inherited Blood Disorders, Orange
RekruttererFase 3
138 Months – 206 Months · Mænd · Opdateret 16. sep. 2026 · NCT07080905

A Study to Investigate the Safety and Effectiveness of a Coagulation Factor IX Gene Insertion Therapy (REGV131-LNP1265) in Pediatric, Adolescent and Adult Participants With Hemophilia B

  • Orthopaedic Hemophilia Treatment Center, Los Angeles
  • David Geffen School of Medicine at UCLA, Los Angeles
  • Children's Hospital Los Angeles, Los Angeles
  • og 2 flere
RekruttererFase 1/2
Alder 2 og opefter · Mænd · Opdateret 11. sep. 2026 · NCT06379789

Efficacy and Safety of CSL222 (Etranacogene Dezaparvovec) Gene Therapy in Adults With Hemophilia B With Pretreatment Adeno-associated Virus Serotype 5 (AAV5) Neutralizing Antibodies (Nabs)

  • University of California, San Diego (UCSD), San Diego
RekruttererFase 3
Alder 18 og opefter · Alle køn · Opdateret 27. aug. 2026 · NCT06003387

ATHN Transcends: A Natural History Study of Non-Neoplastic Hematologic Disorders

  • Orthopaedic Institute for Children HTC, Los Angeles
  • Childrens Hospital Los Angeles, Los Angeles
  • UCSF Benioff Children's Hospital Oakland, Oakland
  • og 5 flere
RekruttererObservationsstudie
Alle aldre · Alle køn · Opdateret 17. aug. 2026 · NCT04398628

A Study of Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of SR604 in Two Participants Groups (Part A: Healthy Participants, and Part B: Participants With Hemophilia A or Hemophilia B or Factor VII Deficiency)

  • Children's Hospital Los Angeles, Los Angeles
RekruttererFase 1Frivillige med god helbredstilstand velkomne
Alder 18 til 60 · Alle køn · Opdateret 2. jul. 2026 · NCT06349473

SEVENFACT® for Bleeding Events in Hemophilia With Inhibitors

  • Orthopaedic Institute for Children, Los Angeles
  • University of California at Davis UC Davis Hemostasis and Thrombosis Center, Sacramento
RekruttererFase 4
Alder 12 til 100 · Alle køn · Opdateret 12. jan. 2026 · NCT04647227

Fra ClinicalTrials.gov, data hentet 5. okt. 2026. Hver studie har sine egne kvalifikationskrav; studieteamet afgør, hvem der kan deltage.