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Hæmofili B kliniske forsøg i Ohio

3 studier for Hæmofili B søger deltagere på steder i Ohio.

Officiel studietekst (engelsk)

A Study to Investigate the Safety and Effectiveness of a Coagulation Factor IX Gene Insertion Therapy (REGV131-LNP1265) in Pediatric, Adolescent and Adult Participants With Hemophilia B

  • Nationwide Children's Hospital, Columbus
RekruttererFase 1/2
Alder 2 og opefter · Mænd · Opdateret 11. sep. 2026 · NCT06379789

ATHN Transcends: A Natural History Study of Non-Neoplastic Hematologic Disorders

  • Akron Children's Hospital - Showers Center for Cancer & Blood Disorders, Akron
  • Cincinnati Children's Hospital Medical Center, Hemophilia & Thrombosis Center, Cincinnati
  • University of Cincinnati Medical Center Hemophilia Treatment Center, Cincinnati
  • og 5 flere
RekruttererObservationsstudie
Alle aldre · Alle køn · Opdateret 17. aug. 2026 · NCT04398628

SEVENFACT® for Bleeding Events in Hemophilia With Inhibitors

  • University Hospitals Health System Cleveland, Cleveland
RekruttererFase 4
Alder 12 til 100 · Alle køn · Opdateret 12. jan. 2026 · NCT04647227

Fra ClinicalTrials.gov, data hentet 5. okt. 2026. Hver studie har sine egne kvalifikationskrav; studieteamet afgør, hvem der kan deltage.