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Medfødte metaboliske sygdomme kliniske forsøg i Californien

5 studier for Medfødte metaboliske sygdomme søger deltagere på steder i Californien.

Byer i Californien

Officiel studietekst (engelsk)

A Long-Term Observational Study of Patients With Fucosidosis

  • Children's Hospital of Orange County, Orange
RekruttererObservationsstudie
Alle aldre · Alle køn · Opdateret 17. sep. 2026 · NCT07615400

Registry of Patients Diagnosed With Lysosomal Storage Diseases

  • University of California San Francisco, San Francisco
RekruttererObservationsstudie
Op til 64 år · Alle køn · Opdateret 8. apr. 2026 · NCT05619900

A Study to Assess the Long-term Safety and Clinical Activity of mRNA-3927 in Participants Previously Enrolled in the mRNA-3927-P101 Study

  • Ronald Reagan UCLA Medical Center, Los Angeles
  • University of Stanford Medical Center, Palo Alto
RekruttererFase 1/2
Alder 1 og opefter · Alle køn · Opdateret 23. mar. 2026 · NCT05130437

Open-Label Study of mRNA-3927 in Participants With Propionic Acidemia

  • UCSD Altman Clinical and Transalational Research Institute Building, Los Angeles
  • Ronald Reagan UCLA Medical Center, Los Angeles
  • Lucile Packard Children's Hospital Stanford, Stanford
RekruttererFase 1/2
Alle aldre · Alle køn · Opdateret 22. jan. 2026 · NCT04159103

An Extension Study to Evaluate the Long-Term Safety and Clinical Activity of mRNA-3705 in Participants Previously Enrolled in Other Clinical Studies of mRNA-3705

  • UCLA Medical Center, Los Angeles
  • Lucile Packard Children's Hospital at Stanford, Palo Alto
  • Altman Clinical and Translational Research Institution, San Diego
RekruttererFase 1/2
Alder 1 og opefter · Alle køn · Opdateret 23. dec. 2025 · NCT05295433

Fra ClinicalTrials.gov, data hentet 3. okt. 2026. Hver studie har sine egne kvalifikationskrav; studieteamet afgør, hvem der kan deltage.