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Metaboliske lidelser kliniske forsøg i Pennsylvania
5 studier for Metaboliske lidelser søger deltagere på steder i Pennsylvania.
Byer i Pennsylvania
Officiel studietekst (engelsk)
Natural History, Physiology, Microbiome and Biochemistry Studies of Propionic Acidemia
- Children's Hospital of Pittsburgh, Pittsburgh
RekruttererObservationsstudieFrivillige med god helbredstilstand velkomne
1 Month – 100 Years · Alle køn · Opdateret 28. sep. 2026 · NCT02890342Clinical and Laboratory Study of Methylmalonic Acidemia
- UPMC Children's Hospital of Pittsburgh, Pittsburgh
RekruttererObservationsstudieFrivillige med god helbredstilstand velkomne
1 Month – 115 Years · Alle køn · Opdateret 10. sep. 2026 · NCT00078078A Study to Evaluate the Efficacy and Safety of Pegozafermin in Participants With Compensated Cirrhosis Due to MASH
- 89bio Clinical Study Site, Philadelphia
- 89bio Clinical Study Site, Pittsburgh
RekruttererFase 3
Alder 18 til 75 · Alle køn · Opdateret 3. sep. 2026 · NCT06419374A Study to Assess the Long-term Safety and Clinical Activity of mRNA-3927 in Participants Previously Enrolled in the mRNA-3927-P101 Study
- The Children's Hospital of Philadelphia (CHOP), Philadelphia
RekruttererFase 1/2
Alder 1 og opefter · Alle køn · Opdateret 23. mar. 2026 · NCT05130437Open-Label Study of mRNA-3927 in Participants With Propionic Acidemia
- Children's Hospital of Philadelphia (CHOP), Philadelphia
RekruttererFase 1/2
Alle aldre · Alle køn · Opdateret 22. jan. 2026 · NCT04159103Fra ClinicalTrials.gov, data hentet 5. okt. 2026. Hver studie har sine egne kvalifikationskrav; studieteamet afgør, hvem der kan deltage.