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Spinal muskelatrofi kliniske forsøg i Arkansas
4 studier for Spinal muskelatrofi søger deltagere på steder i Arkansas.
Byer i Arkansas
Officiel studietekst (engelsk)
A Study Evaluating the Effectiveness and Safety of Risdiplam Administered as an Early Intervention in Pediatric Participants With Spinal Muscular Atrophy After Gene Therapy
- University of Arkansas for Medical Sciences, Little Rock
RekruttererFase 4
3 Months – 24 Months · Alle køn · Opdateret 2. okt. 2026 · NCT05861986A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophy
- Arkansas Children's Hospital, Little Rock
RekruttererFase 2
Alder 5 til 17 · Alle køn · Opdateret 14. sep. 2026 · NCT07287982A Study Evaluating the Effectiveness and Safety of Risdiplam Administered in Pediatric Patients With Spinal Muscular Atrophy Who Experienced a Plateau or Decline in Function After Gene Therapy
- University of Arkansas for Medical Sciences, Little Rock
RekruttererFase 4
3 Months – 24 Months · Alle køn · Opdateret 10. sep. 2026 · NCT05861999Registry of Patients With a Diagnosis of Spinal Muscular Atrophy (SMA)
- Arkansas Children's Hospital, Little Rock
RekruttererObservationsstudie
Alle aldre · Alle køn · Opdateret 31. jan. 2025 · NCT04174157Fra ClinicalTrials.gov, data hentet 5. okt. 2026. Hver studie har sine egne kvalifikationskrav; studieteamet afgør, hvem der kan deltage.