🔎 Trials Near Me

Hjem › Spinal muskelatrofi › Arkansas

Spinal muskelatrofi kliniske forsøg i Arkansas

4 studier for Spinal muskelatrofi søger deltagere på steder i Arkansas.

Byer i Arkansas

Officiel studietekst (engelsk)

A Study Evaluating the Effectiveness and Safety of Risdiplam Administered as an Early Intervention in Pediatric Participants With Spinal Muscular Atrophy After Gene Therapy

  • University of Arkansas for Medical Sciences, Little Rock
RekruttererFase 4
3 Months – 24 Months · Alle køn · Opdateret 2. okt. 2026 · NCT05861986

A Study Evaluating the Effectiveness and Safety of Risdiplam Administered in Pediatric Patients With Spinal Muscular Atrophy Who Experienced a Plateau or Decline in Function After Gene Therapy

  • University of Arkansas for Medical Sciences, Little Rock
RekruttererFase 4
3 Months – 24 Months · Alle køn · Opdateret 10. sep. 2026 · NCT05861999

Registry of Patients With a Diagnosis of Spinal Muscular Atrophy (SMA)

  • Arkansas Children's Hospital, Little Rock
RekruttererObservationsstudie
Alle aldre · Alle køn · Opdateret 31. jan. 2025 · NCT04174157

Fra ClinicalTrials.gov, data hentet 5. okt. 2026. Hver studie har sine egne kvalifikationskrav; studieteamet afgør, hvem der kan deltage.