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Spinal muskelatrofi kliniske forsøg i Colorado

4 studier for Spinal muskelatrofi søger deltagere på steder i Colorado.

Byer i Colorado

Officiel studietekst (engelsk)

A Study Evaluating the Effectiveness and Safety of Risdiplam Administered as an Early Intervention in Pediatric Participants With Spinal Muscular Atrophy After Gene Therapy

  • Children's Hospital of Colorado, Aurora
RekruttererFase 4
3 Months – 24 Months · Alle køn · Opdateret 2. okt. 2026 · NCT05861986

A Study to Evaluate How Apitegromab Works in Subjects Who Are Less Than 2 Years Old and Have Spinal Muscular Atrophy

  • Children's Hospital Colorado, Aurora
RekruttererFase 2
Op til 2 år · Alle køn · Opdateret 2. okt. 2026 · NCT07047144

A Study Evaluating the Effectiveness and Safety of Risdiplam Administered in Pediatric Patients With Spinal Muscular Atrophy Who Experienced a Plateau or Decline in Function After Gene Therapy

  • Children's Hospital of Colorado, Aurora
RekruttererFase 4
3 Months – 24 Months · Alle køn · Opdateret 10. sep. 2026 · NCT05861999

Registry of Patients With a Diagnosis of Spinal Muscular Atrophy (SMA)

  • Children's Hospital Colorado, Aurora
RekruttererObservationsstudie
Alle aldre · Alle køn · Opdateret 31. jan. 2025 · NCT04174157

Fra ClinicalTrials.gov, data hentet 5. okt. 2026. Hver studie har sine egne kvalifikationskrav; studieteamet afgør, hvem der kan deltage.