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Spinal muskelatrofi kliniske forsøg i Iowa

3 studier for Spinal muskelatrofi søger deltagere på steder i Iowa.

Byer i Iowa

Officiel studietekst (engelsk)

A Study to Evaluate How Apitegromab Works in Subjects Who Are Less Than 2 Years Old and Have Spinal Muscular Atrophy

  • University of Iowa, Iowa City
RekruttererFase 2
Op til 2 år · Alle køn · Opdateret 2. okt. 2026 · NCT07047144

A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophy

  • University of Iowa Stead Family Children's Hospital, Iowa City
RekruttererFase 2
Alder 5 til 17 · Alle køn · Opdateret 14. sep. 2026 · NCT07287982

Registry of Patients With a Diagnosis of Spinal Muscular Atrophy (SMA)

  • University of Iowa, Iowa City
RekruttererObservationsstudie
Alle aldre · Alle køn · Opdateret 31. jan. 2025 · NCT04174157

Fra ClinicalTrials.gov, data hentet 5. okt. 2026. Hver studie har sine egne kvalifikationskrav; studieteamet afgør, hvem der kan deltage.