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Spinal muskelatrofi kliniske forsøg i Missouri
4 studier for Spinal muskelatrofi søger deltagere på steder i Missouri.
Byer i Missouri
Officiel studietekst (engelsk)
A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophy
- The Curators of the University of Missouri on behalf of University of Missouri Health Care, Columbia
RekruttererFase 2
Alder 5 til 17 · Alle køn · Opdateret 14. sep. 2026 · NCT07287982ALS/MND Natural History Study Data Repository
- Saint Louis University, St Louis
RekruttererObservationsstudie
Alder 18 til 90 · Alle køn · Opdateret 20. maj 2026 · NCT05966038Effects of Whole-body Electrical Muscle Stimulation Exercise on Adults With Neuromuscular Disease
- NextGen Precision Health Building, Clinical and Translational Science Unit, Columbia
Rekrutterer
Alder 18 og opefter · Alle køn · Opdateret 17. mar. 2026 · NCT07478172Registry of Patients With a Diagnosis of Spinal Muscular Atrophy (SMA)
- University of Missouri Health System, Columbia
- Washington University School of Medicine in St. Louis, St Louis
RekruttererObservationsstudie
Alle aldre · Alle køn · Opdateret 31. jan. 2025 · NCT04174157Fra ClinicalTrials.gov, data hentet 5. okt. 2026. Hver studie har sine egne kvalifikationskrav; studieteamet afgør, hvem der kan deltage.