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Spinal muskelatrofi kliniske forsøg i Virginia

7 studier for Spinal muskelatrofi søger deltagere på steder i Virginia.

Byer i Virginia

Officiel studietekst (engelsk)

A Study to Find Out How Nusinersen is Processed in the Body When Given Through the ThecaFlex DRx™ System in Adult and Pediatric Participants With Spinal Muscular Atrophy (PIERRE-PK)

  • Stacey Hall Developmental Pediatrics, Charlottesville
  • Children's Hospital of the King's Daughters_Norfolk, Norfolk
RekruttererFase 1
Alder 3 og opefter · Alle køn · Opdateret 3. sep. 2026 · NCT06555419

Study of an Intrathecal Port and Catheter System for Subjects With Spinal Muscular Atrophy

  • University of Virginia, Charlottesville
  • Childrens Hospital of the King's Daughters, Norfolk
Rekrutterer
Alder 3 og opefter · Alle køn · Opdateret 19. aug. 2026 · NCT05866419

A Study to Learn About Salanersen's (BIIB115) Effects on Movement and Its Safety When Given Before Symptoms Appear in Babies With Genetically Diagnosed Spinal Muscular Atrophy (SMA)

  • Childrens Hospital of the Kings Daughter Norfolk, Norfolk
RekruttererFase 3
0 Days – 42 Days · Alle køn · Opdateret 18. aug. 2026 · NCT07221669

ALS/MND Natural History Study Data Repository

  • Virginia Commonwealth University, Richmond
RekruttererObservationsstudie
Alder 18 til 90 · Alle køn · Opdateret 20. maj 2026 · NCT05966038

Registry of Patients With a Diagnosis of Spinal Muscular Atrophy (SMA)

  • University of Virginia Health System, Charlottesville
  • Children's Hospital of The King's Daughters, Norfolk
  • Virginia Commonwealth University Health System, Richmond
RekruttererObservationsstudie
Alle aldre · Alle køn · Opdateret 31. jan. 2025 · NCT04174157

Fra ClinicalTrials.gov, data hentet 5. okt. 2026. Hver studie har sine egne kvalifikationskrav; studieteamet afgør, hvem der kan deltage.