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Thalassæmi kliniske forsøg i New York

4 studier for Thalassæmi søger deltagere på steder i New York.

Byer i New York

Officiel studietekst (engelsk)

A Research Study Looking at Long-term Treatment With Etavopivat in People With Sickle Cell Disease or Thalassaemia

  • Columbia University Medical Center_New York_0, New York
  • Columbia University Medical Center_New York_0, New York
RekruttererFase 3
Alder 2 og opefter · Alle køn · Opdateret 18. sep. 2026 · NCT06609226

ATHN Transcends: A Natural History Study of Non-Neoplastic Hematologic Disorders

  • Western New York BloodCare, Buffalo
  • Northwell Health Hemostasis and Thrombosis Center at Long Island Jewish and Cohen Children's Medical Center, Hyde Park
  • Weill Cornell Medical College - New York Presbyterian Hospital, New York
  • og 2 flere
RekruttererObservationsstudie
Alle aldre · Alle køn · Opdateret 17. aug. 2026 · NCT04398628

A Study of Immune Suppression Treatment for People With Sickle Cell Disease or β-Thalassemia Who Are Going to Receive an Allogeneic Hematopoietic Cell Transplantation (HCT)

  • Memorial Sloan Kettering Suffolk - Commack (Consent only), Commack
  • Memorial Sloan Kettering Westchester (Consent only), Harrison
  • Memorial Sloan Kettering Nassau (All protocol activities), Rockville Centre
RekruttererFase 2
Alder 2 til 50 · Alle køn · Opdateret 3. jun. 2026 · NCT05736419

Evaluation of Efficacy and Safety of a Single Dose of CTX001 in Participants With Transfusion-Dependent β-Thalassemia and Severe Sickle Cell Disease

  • New York Presbyterian Hospital - Morgan Stanley Children's Hospital, New York
RekruttererFase 3
Alder 12 til 35 · Alle køn · Opdateret 23. mar. 2026 · NCT05477563

Fra ClinicalTrials.gov, data hentet 5. okt. 2026. Hver studie har sine egne kvalifikationskrav; studieteamet afgør, hvem der kan deltage.