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Thalassæmi kliniske forsøg i North Carolina

3 studier for Thalassæmi søger deltagere på steder i North Carolina.

Byer i North Carolina

Officiel studietekst (engelsk)

A Research Study Looking at Long-term Treatment With Etavopivat in People With Sickle Cell Disease or Thalassaemia

  • Atrium Levine Children's/Atrium Health, Charlotte
  • Duke University_Durham, Durham
RekruttererFase 3
Alder 2 og opefter · Alle køn · Opdateret 18. sep. 2026 · NCT06609226

ATHN Transcends: A Natural History Study of Non-Neoplastic Hematologic Disorders

  • Comprehensive Hemophilia Treatment Center, University of North Carolina at Chapel Hill, Chapel Hill
  • St. Jude Affiliate Clinic at Novant Health Hemby Children's Hospital, Charlotte
  • East Carolina University Hemophilia Treatment Center, Greenville
  • og 1 flere
RekruttererObservationsstudie
Alle aldre · Alle køn · Opdateret 17. aug. 2026 · NCT04398628

Evaluation of Efficacy and Safety of a Single Dose of CTX001 in Participants With Transfusion-Dependent β-Thalassemia and Severe Sickle Cell Disease

  • Levine Children's Hospital - Hematology, Charlotte
RekruttererFase 3
Alder 12 til 35 · Alle køn · Opdateret 23. mar. 2026 · NCT05477563

Fra ClinicalTrials.gov, data hentet 5. okt. 2026. Hver studie har sine egne kvalifikationskrav; studieteamet afgør, hvem der kan deltage.