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Ensayos clínicos de Atrofia muscular espinal en Georgia

3 estudios sobre Atrofia muscular espinal buscan participantes en Georgia.

Ciudades en Georgia

Texto oficial del estudio (inglés)

A Study to Evaluate How Apitegromab Works in Subjects Who Are Less Than 2 Years Old and Have Spinal Muscular Atrophy

  • Children's Healthcare of Atlanta, Atlanta
ReclutandoFase 2
Hasta los 2 · Todos los sexos · Actualizado el 14 sept 2026 · NCT07047144

A Study Evaluating the Effectiveness and Safety of Risdiplam Administered in Pediatric Patients With Spinal Muscular Atrophy Who Experienced a Plateau or Decline in Function After Gene Therapy

  • Children's Healthcare of Atlanta Center for Advanced Pediatrics, Atlanta
ReclutandoFase 4
3 Months – 24 Months · Todos los sexos · Actualizado el 10 sept 2026 · NCT05861999

A Study Evaluating the Effectiveness and Safety of Risdiplam Administered as an Early Intervention in Pediatric Participants With Spinal Muscular Atrophy After Gene Therapy

  • Children's Healthcare of Atlanta Center for Advanced Pediatrics, Atlanta
ReclutandoFase 4
3 Months – 24 Months · Todos los sexos · Actualizado el 3 sept 2026 · NCT05861986

De ClinicalTrials.gov, datos obtenidos el 1 oct 2026. Cada estudio establece sus propios criterios de elegibilidad; el equipo del estudio decide quién puede participar.