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Duchenne Muscular Dystrophy clinical trials in Missouri

3 studies for Duchenne Muscular Dystrophy are looking for participants at sites in Missouri.

Cities in Missouri

A Study of SGT-003 Gene Therapy in Duchenne Muscular Dystrophy (INSPIRE DUCHENNE)

  • Washington University in St. Louis, St Louis
RecruitingPhase 1/2
Ages 0 to 17 · Men · Updated Jul 8, 2026 · NCT06138639

PBGENE-DMD Phase 1/2a Safety and Preliminary Efficacy Study in Duchenne Muscular Dystrophy (FUNCTION-DMD)

  • Washington University School of Medicine, St Louis
RecruitingPhase 1/2
Ages 2 to 7 · Men · Updated Jun 23, 2026 · NCT07429240

From ClinicalTrials.gov, data retrieved Oct 5, 2026. Each study sets its own eligibility; the study team decides who can join.