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Seljaaju-lihasatroofia kliinilised uuringud osariigis Illinois

6 uuringut haiguse Seljaaju-lihasatroofia jaoks otsivad osalejaid osariigis Illinois.

Linnad osariigis Illinois

Ametlik uuringutekst (inglise keeles)

A Study Evaluating the Effectiveness and Safety of Risdiplam Administered as an Early Intervention in Pediatric Participants With Spinal Muscular Atrophy After Gene Therapy

  • Ann and Robert H. Lurie Children Hospital of Chicago, Chicago
VärbamineFaas 4
3 Months – 24 Months · Kõik sood · Uuendatud 2. okt 2026 · NCT05861986

A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophy

  • Ann & Robert H. Lurie Children's Hospital of Chicago, Chicago
VärbamineFaas 2
Vanused 5–17 · Kõik sood · Uuendatud 14. sept 2026 · NCT07287982

A Study to Find Out How Nusinersen is Processed in the Body When Given Through the ThecaFlex DRx™ System in Adult and Pediatric Participants With Spinal Muscular Atrophy (PIERRE-PK)

  • Ann & Robert H. Lurie Children's Hospital of Chicago, Chicago
VärbamineFaas 1
Vanused 3 ja vanemad · Kõik sood · Uuendatud 3. sept 2026 · NCT06555419

Study of an Intrathecal Port and Catheter System for Subjects With Spinal Muscular Atrophy

  • Lurie Childrens Hospital, Chicago
Värbamine
Vanused 3 ja vanemad · Kõik sood · Uuendatud 19. aug 2026 · NCT05866419

A Study to Learn About Salanersen's (BIIB115) Effects on Movement and Its Safety When Given Before Symptoms Appear in Babies With Genetically Diagnosed Spinal Muscular Atrophy (SMA)

  • Ann and Robert H Lurie Childrens Hospital of Chicago, Chicago
VärbamineFaas 3
0 Days – 42 Days · Kõik sood · Uuendatud 18. aug 2026 · NCT07221669

ALS/MND Natural History Study Data Repository

  • Northwestern University, Chicago
VärbamineVaatlusuuring
Vanused 18–90 · Kõik sood · Uuendatud 20. mai 2026 · NCT05966038

Allikas ClinicalTrials.gov, andmed saadud 5. okt 2026. Igal uuringul on oma osalemiskõlblikkuse tingimused; uuringumeeskond otsustab, kes saab osaleda.