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Seljaaju-lihasatroofia kliinilised uuringud osariigis Virginia
7 uuringut haiguse Seljaaju-lihasatroofia jaoks otsivad osalejaid osariigis Virginia.
Linnad osariigis Virginia
Ametlik uuringutekst (inglise keeles)
A Study to Learn About Salanersen's (BIIB115) Effects on Movement and Its Safety in Participants Aged 15 to 60 Years With Spinal Muscular Atrophy (SMA) Who Are Either New to SMA Treatment or Were Previously Treated With Risdiplam
- Childrens Hospital of the Kings Daughter Norfolk, Norfolk
VärbamineFaas 3
Vanused 15–60 · Kõik sood · Uuendatud 2. okt 2026 · NCT07444476A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophy
- Childrens Hospital of The Kings Daughters, Norfolk
VärbamineFaas 2
Vanused 5–17 · Kõik sood · Uuendatud 14. sept 2026 · NCT07287982A Study to Find Out How Nusinersen is Processed in the Body When Given Through the ThecaFlex DRx™ System in Adult and Pediatric Participants With Spinal Muscular Atrophy (PIERRE-PK)
- Stacey Hall Developmental Pediatrics, Charlottesville
- Children's Hospital of the King's Daughters_Norfolk, Norfolk
VärbamineFaas 1
Vanused 3 ja vanemad · Kõik sood · Uuendatud 3. sept 2026 · NCT06555419Study of an Intrathecal Port and Catheter System for Subjects With Spinal Muscular Atrophy
- University of Virginia, Charlottesville
- Childrens Hospital of the King's Daughters, Norfolk
Värbamine
Vanused 3 ja vanemad · Kõik sood · Uuendatud 19. aug 2026 · NCT05866419A Study to Learn About Salanersen's (BIIB115) Effects on Movement and Its Safety When Given Before Symptoms Appear in Babies With Genetically Diagnosed Spinal Muscular Atrophy (SMA)
- Childrens Hospital of the Kings Daughter Norfolk, Norfolk
VärbamineFaas 3
0 Days – 42 Days · Kõik sood · Uuendatud 18. aug 2026 · NCT07221669ALS/MND Natural History Study Data Repository
- Virginia Commonwealth University, Richmond
VärbamineVaatlusuuring
Vanused 18–90 · Kõik sood · Uuendatud 20. mai 2026 · NCT05966038Registry of Patients With a Diagnosis of Spinal Muscular Atrophy (SMA)
- University of Virginia Health System, Charlottesville
- Children's Hospital of The King's Daughters, Norfolk
- Virginia Commonwealth University Health System, Richmond
VärbamineVaatlusuuring
Kõik vanused · Kõik sood · Uuendatud 31. jaan 2025 · NCT04174157Allikas ClinicalTrials.gov, andmed saadud 5. okt 2026. Igal uuringul on oma osalemiskõlblikkuse tingimused; uuringumeeskond otsustab, kes saab osaleda.