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Pag-aaral pangklinika para sa Fabry Disease sa California

3 pag-aaral para sa Fabry Disease ang naghahanap ng mga kalahok sa mga site sa California.

Opisyal na teksto ng pag-aaral (English)

A Study to Learn How Well Lucerastat Works and How Safe it is in Untreated Adult Male Participants With Fabry Disease

  • UCSF Benioff Childens Hospital, Oakland
Nagre-recruitPhase 3
Edad 18 hanggang 60 · Kalalakihan · Na-update Nob 3, 2026 · NCT07778667

Fabry Disease Registry & Pregnancy Sub-registry

  • Southern California Permanente Medical Group- Site Number : 840108, Los Angeles
  • University Of California Los Angeles- Site Number : 840088, Los Angeles
  • Children's Hospital of Orange County- Site Number : 840074, Orange
  • at 4 pa
Nagre-recruitObservasyonal na pag-aaral
Lahat ng edad · Lahat ng kasarian · Na-update Okt 14, 2026 · NCT00196742

Safety, PK/PD, and Exploratory Efficacy Study of AMT-191 in Classic Fabry Disease

  • University of California Los Angeles (UCLA), Los Angeles
Nagre-recruitPhase 1/2
Edad 18 hanggang 65 · Kalalakihan · Na-update Set 24, 2026 · NCT06270316

Mula sa ClinicalTrials.gov, na-kuha noong Nob 15, 2026. Ang bawat pag-aaral ay may sariling pamantayan sa eligibility; ang koponan ng pag-aaral ang magdedesisyon kung sino ang makakasali.