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Pag-aaral pangklinika para sa Fabry Disease sa Ohio

4 pag-aaral para sa Fabry Disease ang naghahanap ng mga kalahok sa mga site sa Ohio.

Mga Lungsod sa Ohio

Opisyal na teksto ng pag-aaral (English)

Safety, PK/PD, and Exploratory Efficacy Study of AMT-191 in Classic Fabry Disease

  • Children's Hospital Medical Center, Cincinnati
Nagre-recruitPhase 1/2
Edad 18 hanggang 65 · Kalalakihan · Na-update Set 24, 2026 · NCT06270316

A Study of Migalastat in Pediatric Subjects (2 to <12 Yrs) With Fabry Disease and Amenable GLA Variants

  • Cincinnati Children's Hospital Medical Center, Cincinnati
Nagre-recruitPhase 3
Edad 2 hanggang 11 · Lahat ng kasarian · Na-update Set 1, 2026 · NCT06904261

A Study to Learn About the Safety and Effects of the Study Drug PRX-102 in Children and Adolescents With Fabry Disease

  • Cincinnati Children's Hospital Medical Center, Cincinnati
Nagre-recruitPhase 2/3
Edad 2 hanggang 17 · Lahat ng kasarian · Na-update Ago 10, 2026 · NCT06328608

Fabry Disease Registry & Pregnancy Sub-registry

  • Cincinnati Children's Hospital Medical Center (Cincinnati Children's Hospital)- Site Number : 840033, Cincinnati
  • University Hospitals Cleveland Medical Center- Site Number : 840119, Cleveland
  • Cleveland Clinic - Cleveland- Site Number : 840048, Cleveland
  • at 2 pa
Nagre-recruitObservasyonal na pag-aaral
Lahat ng edad · Lahat ng kasarian · Na-update Hun 23, 2026 · NCT00196742

Mula sa ClinicalTrials.gov, na-kuha noong Okt 5, 2026. Ang bawat pag-aaral ay may sariling pamantayan sa eligibility; ang koponan ng pag-aaral ang magdedesisyon kung sino ang makakasali.