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Pag-aaral pangklinika para sa Fabry Disease sa Pennsylvania

6 pag-aaral para sa Fabry Disease ang naghahanap ng mga kalahok sa mga site sa Pennsylvania.

Mga Lungsod sa Pennsylvania

Opisyal na teksto ng pag-aaral (English)

A Study to Learn How Well Lucerastat Works and How Safe it is in Untreated Adult Male Participants With Fabry Disease

  • Hospital of University Pennsylvania, Translational Medicine and Human Genetics, Philadelphia
Nagre-recruitPhase 3
Edad 18 hanggang 60 · Kalalakihan · Na-update Nob 3, 2026 · NCT07778667

A Study of Patients With Fabry Disease (US Specific)

  • UPMC Children's Hospital of Pittsburgh, Pittsburgh
Nagre-recruitObservasyonal na pag-aaral
Edad 18 pataas · Lahat ng kasarian · Na-update Okt 28, 2026 · NCT06906367

A Global Prospective Observational Study of Women With Fabry Disease and Their Infants During Pregnancy and Breastfeeding

  • Amicus Therapeutics, Inc. Pregnancy Registry, Philadelphia
Nagre-recruitObservasyonal na pag-aaral
Lahat ng edad · Kababaihan · Na-update Okt 28, 2026 · NCT04252066

A Study of Migalastat in Pediatric Subjects (2 to <12 Yrs) With Fabry Disease and Amenable GLA Variants

  • UPMC Children's Hospital of Pittsburgh, Pittsburgh
Nagre-recruitPhase 3
Edad 2 hanggang 11 · Lahat ng kasarian · Na-update Okt 22, 2026 · NCT06904261

Fabry Disease Registry & Pregnancy Sub-registry

  • Geisinger Medical Center- Site Number : 840111, Danville
  • Penn State University Medical Center-Neurology- Site Number : 840104, Hershey
  • Children'S Hospital Of Philadelphia Hup Medical Genetics- Site Number : 840089, Philadelphia
  • at 2 pa
Nagre-recruitObservasyonal na pag-aaral
Lahat ng edad · Lahat ng kasarian · Na-update Okt 14, 2026 · NCT00196742

Safety, PK/PD, and Exploratory Efficacy Study of AMT-191 in Classic Fabry Disease

  • UPMC Children's Hospital of Pittsburgh, Pittsburgh
Nagre-recruitPhase 1/2
Edad 18 hanggang 65 · Kalalakihan · Na-update Set 24, 2026 · NCT06270316

Mula sa ClinicalTrials.gov, na-kuha noong Nob 15, 2026. Ang bawat pag-aaral ay may sariling pamantayan sa eligibility; ang koponan ng pag-aaral ang magdedesisyon kung sino ang makakasali.