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Pag-aaral pangklinika para sa Fabry Disease sa Pennsylvania
6 pag-aaral para sa Fabry Disease ang naghahanap ng mga kalahok sa mga site sa Pennsylvania.
Mga Lungsod sa Pennsylvania
Opisyal na teksto ng pag-aaral (English)
A Study to Learn How Well Lucerastat Works and How Safe it is in Untreated Adult Male Participants With Fabry Disease
- Hospital of University Pennsylvania, Translational Medicine and Human Genetics, Philadelphia
Nagre-recruitPhase 3
Edad 18 hanggang 60 · Kalalakihan · Na-update Nob 3, 2026 · NCT07778667A Study of Patients With Fabry Disease (US Specific)
- UPMC Children's Hospital of Pittsburgh, Pittsburgh
Nagre-recruitObservasyonal na pag-aaral
Edad 18 pataas · Lahat ng kasarian · Na-update Okt 28, 2026 · NCT06906367A Global Prospective Observational Study of Women With Fabry Disease and Their Infants During Pregnancy and Breastfeeding
- Amicus Therapeutics, Inc. Pregnancy Registry, Philadelphia
Nagre-recruitObservasyonal na pag-aaral
Lahat ng edad · Kababaihan · Na-update Okt 28, 2026 · NCT04252066A Study of Migalastat in Pediatric Subjects (2 to <12 Yrs) With Fabry Disease and Amenable GLA Variants
- UPMC Children's Hospital of Pittsburgh, Pittsburgh
Nagre-recruitPhase 3
Edad 2 hanggang 11 · Lahat ng kasarian · Na-update Okt 22, 2026 · NCT06904261Fabry Disease Registry & Pregnancy Sub-registry
- Geisinger Medical Center- Site Number : 840111, Danville
- Penn State University Medical Center-Neurology- Site Number : 840104, Hershey
- Children'S Hospital Of Philadelphia Hup Medical Genetics- Site Number : 840089, Philadelphia
- at 2 pa
Nagre-recruitObservasyonal na pag-aaral
Lahat ng edad · Lahat ng kasarian · Na-update Okt 14, 2026 · NCT00196742Safety, PK/PD, and Exploratory Efficacy Study of AMT-191 in Classic Fabry Disease
- UPMC Children's Hospital of Pittsburgh, Pittsburgh
Nagre-recruitPhase 1/2
Edad 18 hanggang 65 · Kalalakihan · Na-update Set 24, 2026 · NCT06270316Mula sa ClinicalTrials.gov, na-kuha noong Nob 15, 2026. Ang bawat pag-aaral ay may sariling pamantayan sa eligibility; ang koponan ng pag-aaral ang magdedesisyon kung sino ang makakasali.