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Pag-aaral pangklinika para sa Fabry Disease sa Virginia

6 pag-aaral para sa Fabry Disease ang naghahanap ng mga kalahok sa mga site sa Virginia.

Mga Lungsod sa Virginia

Opisyal na teksto ng pag-aaral (English)

Safety, PK/PD, and Exploratory Efficacy Study of AMT-191 in Classic Fabry Disease

  • Lysosomal & Rare Disorders Research and Treatment Center, Inc, Fairfax
Nagre-recruitPhase 1/2
Edad 18 hanggang 65 · Kalalakihan · Na-update Set 24, 2026 · NCT06270316

A Study of Patients With Fabry Disease (US Specific)

  • Lysosomal and Rare Disorders Research and Treatment Center, Inc., Fairfax
Nagre-recruitObservasyonal na pag-aaral
Edad 18 pataas · Lahat ng kasarian · Na-update Set 9, 2026 · NCT06906367

A Study of Migalastat in Pediatric Subjects (2 to <12 Yrs) With Fabry Disease and Amenable GLA Variants

  • Lysosomal and Rare Disorders Research and Treatment Center, Inc., Fairfax
Nagre-recruitPhase 3
Edad 2 hanggang 11 · Lahat ng kasarian · Na-update Set 1, 2026 · NCT06904261

A Study to Learn About the Safety and Effects of the Study Drug PRX-102 in Children and Adolescents With Fabry Disease

  • Lysosomal and Rare Disorders Research and Treatment Center Inc, Fairfax
Nagre-recruitPhase 2/3
Edad 2 hanggang 17 · Lahat ng kasarian · Na-update Ago 10, 2026 · NCT06328608

Fabry Disease Registry & Pregnancy Sub-registry

  • O & O Alpan- Site Number : 840025, Fairfax
Nagre-recruitObservasyonal na pag-aaral
Lahat ng edad · Lahat ng kasarian · Na-update Hun 23, 2026 · NCT00196742

A Multi-Country Observational Study of Safety and Effectiveness of Elfabrio® in Fabry Patients

  • Lysosomal & Rare Disorder Research & Treatment Center (LRDRTC), Fairfax
Nagre-recruitObservasyonal na pag-aaral
Edad 18 pataas · Lahat ng kasarian · Na-update Nob 14, 2025 · NCT06663358

Mula sa ClinicalTrials.gov, na-kuha noong Okt 5, 2026. Ang bawat pag-aaral ay may sariling pamantayan sa eligibility; ang koponan ng pag-aaral ang magdedesisyon kung sino ang makakasali.