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Pag-aaral pangklinika para sa Familial Amyloid Neuropathies na nagre-recruit sa U.S.

17 pag-aaral para sa Familial Amyloid Neuropathies ang nagre-recruit ng mga kalahok sa mga site sa buong Estados Unidos.

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Opisyal na teksto ng pag-aaral (English)

Non-interventional Study of Patients With Transthyretin (ATTR) Amyloidosis

Nagre-recruitObservasyonal na pag-aaral
Edad 18 hanggang 130 · Lahat ng kasarian · Na-update Set 23, 2026 · NCT06465810

Patisiran-Lipid Nanoparticle (LNP) Pregnancy Surveillance Program

Nagre-recruitObservasyonal na pag-aaral
Lahat ng edad · Kababaihan · Na-update Set 8, 2026 · NCT05040373

ConTTRibute: A Global Observational Study of Patients With Transthyretin (TTR)-Mediated Amyloidosis (ATTR Amyloidosis)

Nagre-recruitObservasyonal na pag-aaral
Lahat ng edad · Lahat ng kasarian · Na-update Set 8, 2026 · NCT04561518

Subclinical Transthyretin Cardiac Amyloidosis in V122I TTR Carriers

Nagre-recruitObservasyonal na pag-aaral
Edad 30 hanggang 80 · Lahat ng kasarian · Na-update Ago 31, 2026 · NCT05489549

Ultrasound Therapy In Cardiac Amyloidosis

Nagre-recruitPhase 4Malugod na tinatanggap ang malusog na boluntaryo
Edad 18 hanggang 90 · Lahat ng kasarian · Na-update Ago 21, 2026 · NCT04667494

Cardiovascular Multimodality Imaging Study

Nagre-recruitObservasyonal na pag-aaral
Edad 18 pataas · Lahat ng kasarian · Na-update Ago 10, 2026 · NCT06610019

Acoramidis Transthyretin Amyloidosis Prevention Trial in the Young (ACT-EARLY) Study in Asymptomatic Carriers of a Pathogenic TTR Variant

Nagre-recruitPhase 3
Edad 18 hanggang 75 · Lahat ng kasarian · Na-update Ago 4, 2026 · NCT06563895

Cardiac Magnetic Resonance and Echocardiography Study With Acoramidis

Nagre-recruitPhase 4
Edad 18 hanggang 80 · Lahat ng kasarian · Na-update Hul 29, 2026 · NCT07695701

Artificial Intelligence Guided Echocardiographic Screening of Rare Diseases (EchoNet-Screening)

Nagre-recruitObservasyonal na pag-aaral
Edad 18 pataas · Lahat ng kasarian · Na-update Hul 22, 2026 · NCT05139797

CAPACITY (Cardiac Amyloidosis and Physical ACtivITY) Study

Nagre-recruit
Edad 18 pataas · Lahat ng kasarian · Na-update Hul 21, 2026 · NCT06096675

[64Cu]FBP8 PET for Early Detection of Intracardiac Thrombus in Amyloid Cardiomyopathy

Nagre-recruitPhase 3
Edad 18 pataas · Lahat ng kasarian · Na-update Hul 21, 2026 · NCT07560306

Analysis of Lumbar Spine Stenosis Specimens for Identification of Transthyretin Cardiac Amyloidosis

Nagre-recruitObservasyonal na pag-aaralMalugod na tinatanggap ang malusog na boluntaryo
Edad 50 pataas · Lahat ng kasarian · Na-update Hun 4, 2026 · NCT06034405

Elevated Rate Pacing of Cardiac Amyloidosis

Nagre-recruit
Edad 18 pataas · Lahat ng kasarian · Na-update May 13, 2026 · NCT07583823

A Study Of Deep Learning For Echo Analysis, Tracking, And Evaluation

Nagre-recruitObservasyonal na pag-aaral
Edad 18 pataas · Lahat ng kasarian · Na-update Abr 16, 2026 · NCT07308704

Determining the Association of TTR Stabilizing Therapy With Circulating TTR Amyloid Aggregates Over Time in Patients With ATTR-CM: Longitudinal Biomarker Study

Nagre-recruitObservasyonal na pag-aaral
Edad 30 hanggang 80 · Lahat ng kasarian · Na-update Ene 7, 2026 · NCT07196839

US Benchmarking Clinical Study

Nagre-recruitObservasyonal na pag-aaralMalugod na tinatanggap ang malusog na boluntaryo
Edad 60 pataas · Lahat ng kasarian · Na-update Okt 20, 2025 · NCT07215715

Exercise Training in Transthyretin Cardiac Amyloidosis

Nagre-recruit
Edad 60 hanggang 90 · Lahat ng kasarian · Na-update Mar 18, 2025 · NCT05797857

Mula sa ClinicalTrials.gov, na-kuha noong Okt 5, 2026. Ang bawat pag-aaral ay may sariling pamantayan sa eligibility; ang koponan ng pag-aaral ang magdedesisyon kung sino ang makakasali.