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Pag-aaral pangklinika para sa Genetic Disorders sa New York

8 pag-aaral para sa Genetic Disorders ang naghahanap ng mga kalahok sa mga site sa New York.

Mga Lungsod sa New York

Opisyal na teksto ng pag-aaral (English)

A Phase 3 Evaluation of Sutacimig in Glanzmann Thrombasthenia

  • New York-Presbyterian - Weill Cornell Medical Center, New York
Nagre-recruitPhase 3
Edad 12 hanggang 70 · Lahat ng kasarian · Na-update Nob 13, 2026 · NCT07935356

Helix Research Network

  • Rochester Regional Health (GenoWell), Rochester
Nagre-recruitObservasyonal na pag-aaralMalugod na tinatanggap ang malusog na boluntaryo
Edad 18 pataas · Lahat ng kasarian · Na-update Nob 12, 2026 · NCT06057181

Long-term Follow-up (LTFU) Study of Participants in Any iECURE Protocol Using an Investigational Product (IP)

  • Icahn School of Medicine at Mount Sinai, New York
Nagre-recruitObservasyonal na pag-aaral
7 Months – 15 Months · Lahat ng kasarian · Na-update Nob 5, 2026 · NCT06805695

Safety of Anumigilimab (CSL324) in Adults With Sickle Cell Disease (SCD)

  • NYC Health + Hospitals/Queens, Jamaica
  • Columbia University Medical Center, New York
  • Jacobi Medical Center, The Bronx
Nagre-recruitPhase 2
Edad 18 pataas · Lahat ng kasarian · Na-update Nob 3, 2026 · NCT07224360

A Study to Assess the Long-term Safety and Clinical Activity of mRNA-3927 in Participants Previously Enrolled in the mRNA-3927-P101 Study

  • Icahn School of Medicine at Mount Sinai, New York
Nagre-recruitPhase 1/2
Edad 1 pataas · Lahat ng kasarian · Na-update Mar 23, 2026 · NCT05130437

Evaluation of Efficacy and Safety of a Single Dose of CTX001 in Participants With Transfusion-Dependent β-Thalassemia and Severe Sickle Cell Disease

  • New York Presbyterian Hospital - Morgan Stanley Children's Hospital, New York
Nagre-recruitPhase 3
Edad 12 hanggang 35 · Lahat ng kasarian · Na-update Mar 23, 2026 · NCT05477563

Open-Label Study of mRNA-3927 in Participants With Propionic Acidemia

  • Icahn School of Medicine at Mount Sinai - Clinical Research Unit, New York
Nagre-recruitPhase 1/2
Lahat ng edad · Lahat ng kasarian · Na-update Ene 22, 2026 · NCT04159103

STXBP1 and SYNGAP1 Related Disorders Natural History Study

  • Weill Cornell Medicine, New York
Nagre-recruitObservasyonal na pag-aaral
Lahat ng edad · Lahat ng kasarian · Na-update Okt 29, 2025 · NCT06555965

Mula sa ClinicalTrials.gov, na-kuha noong Nob 15, 2026. Ang bawat pag-aaral ay may sariling pamantayan sa eligibility; ang koponan ng pag-aaral ang magdedesisyon kung sino ang makakasali.