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Pag-aaral pangklinika para sa Genetic Disorders sa North Carolina

10 pag-aaral para sa Genetic Disorders ang naghahanap ng mga kalahok sa mga site sa North Carolina.

Mga Lungsod sa North Carolina

Opisyal na teksto ng pag-aaral (English)

A Phase 3 Evaluation of Sutacimig in Glanzmann Thrombasthenia

  • Science 37, Durham
Nagre-recruitPhase 3
Edad 12 hanggang 70 · Lahat ng kasarian · Na-update Nob 13, 2026 · NCT07935356

Helix Research Network

  • Cone Health (Gene Connect), Burlington
  • WakeMed (PreciselyYou), Raleigh
Nagre-recruitObservasyonal na pag-aaralMalugod na tinatanggap ang malusog na boluntaryo
Edad 18 pataas · Lahat ng kasarian · Na-update Nob 12, 2026 · NCT06057181

Clinical and Genetic Evaluation of Individuals With Undiagnosed Disorders Through the Undiagnosed Diseases Network

  • Duke University Health System, Durham
Nagre-recruitObservasyonal na pag-aaralMalugod na tinatanggap ang malusog na boluntaryo
1 Month – 100 Years · Lahat ng kasarian · Na-update Nob 3, 2026 · NCT02450851

Inherited Reproductive Disorders

  • NIEHS Clinical Research Unit (CRU), Research Triangle Park
Nagre-recruitObservasyonal na pag-aaral
6 Weeks – 120 Years · Lahat ng kasarian · Na-update Okt 26, 2026 · NCT01500447

PKP2-ACM Natural History Study

  • Duke University, Durham
Nagre-recruitObservasyonal na pag-aaral
Edad 12 pataas · Lahat ng kasarian · Na-update Okt 14, 2026 · NCT06644742

Rett Syndrome Registry

  • The University of North Carolina at Chapel Hill, Chapel Hill
Nagre-recruitObservasyonal na pag-aaral
Edad 0 hanggang 99 · Lahat ng kasarian · Na-update Hun 30, 2026 · NCT05432349

Efficacy, Safety, and Tolerability of Zeleciment Rostudirsen (DYNE-251) Administered Intravenously Every 4 Weeks in Ambulatory Participants With Duchenne Muscular Dystrophy (FORZETTO)

  • Rare Disease Research, LLC, Hillsborough
Nagre-recruitPhase 3
Edad 4 hanggang 18 · Kalalakihan · Na-update May 27, 2026 · NCT07608432

A Study to Assess the Long-term Safety and Clinical Activity of mRNA-3927 in Participants Previously Enrolled in the mRNA-3927-P101 Study

  • Duke University Medical System (Duke Health), Durham
Nagre-recruitPhase 1/2
Edad 1 pataas · Lahat ng kasarian · Na-update Mar 23, 2026 · NCT05130437

Evaluation of Efficacy and Safety of a Single Dose of CTX001 in Participants With Transfusion-Dependent β-Thalassemia and Severe Sickle Cell Disease

  • Levine Children's Hospital - Hematology, Charlotte
Nagre-recruitPhase 3
Edad 12 hanggang 35 · Lahat ng kasarian · Na-update Mar 23, 2026 · NCT05477563

Open-Label Study of mRNA-3927 in Participants With Propionic Acidemia

  • Duke University Medical System (Duke Health), Durham
Nagre-recruitPhase 1/2
Lahat ng edad · Lahat ng kasarian · Na-update Ene 22, 2026 · NCT04159103

Mula sa ClinicalTrials.gov, na-kuha noong Nob 15, 2026. Ang bawat pag-aaral ay may sariling pamantayan sa eligibility; ang koponan ng pag-aaral ang magdedesisyon kung sino ang makakasali.