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Pag-aaral pangklinika para sa Sakit sa Pag-iimbak ng Glycogen Uri II sa North Carolina

8 pag-aaral para sa Sakit sa Pag-iimbak ng Glycogen Uri II ang naghahanap ng mga kalahok sa mga site sa North Carolina.

Mga Lungsod sa North Carolina

Opisyal na teksto ng pag-aaral (English)

A Study to Evaluate the Safety, Pharmacokinetics, and Pharmacodynamics of DNL952 in Adult Participants With Late-Onset Pompe Disease

  • Duke University School of Medicine - Early Phase Research Unit, Durham
Nagre-recruitPhase 1
Edad 18 hanggang 75 · Lahat ng kasarian · Na-update Ago 17, 2026 · NCT07354724

A Study to Evaluate Safety, Tolerability, and Efficacy of AB-1009 Gene Therapy (GAA Gene) in Adult Participants With Late-Onset Pompe Disease (PROGRESS-GT LOPD)

  • Duke University, Durham
Nagre-recruitPhase 1/2
Edad 18 hanggang 65 · Lahat ng kasarian · Na-update Hul 20, 2026 · NCT07282847

Study of S-606001 as an Add-on to Enzyme Replacement Therapy (ERT) in Participants With Late-onset Pompe Disease (LOPD)

  • Duke University Medical Center, Durham
Nagre-recruitPhase 2
Edad 18 pataas · Lahat ng kasarian · Na-update Hun 23, 2026 · NCT07123155

Pompe Disease Registry Protocol

  • Carolinas Medical Center Hospital- Site Number : 840065, Charlotte
  • Duke University Medical Center Genetics Dept- Site Number : 840037, Durham
Nagre-recruitObservasyonal na pag-aaral
Lahat ng edad · Lahat ng kasarian · Na-update Hun 23, 2026 · NCT00231400

Pompe Pregnancy Sub-Registry

  • Duke University Medical Center Genetics Dept- Site Number : 840037, Durham
Nagre-recruitObservasyonal na pag-aaral
Lahat ng edad · Kababaihan · Na-update Abr 16, 2026 · NCT00567073

Determination of CRIM Status and Longitudinal Follow-up of Individuals With Pompe Disease

  • Duke University Medical Center, Durham
Nagre-recruitObservasyonal na pag-aaral
Lahat ng edad · Lahat ng kasarian · Na-update Abr 8, 2026 · NCT01665326

A Global Prospective Observational Registry of Patients With Pompe Disease

  • Duke University Medical Center, Durham
Nagre-recruitObservasyonal na pag-aaral
Lahat ng edad · Lahat ng kasarian · Na-update Mar 10, 2026 · NCT06121011

Cognitive and Neurological Pathologies in Pompe Disease

  • Duke University Medical Center, Durham
Nagre-recruitObservasyonal na pag-aaral
Edad 0 hanggang 18 · Lahat ng kasarian · Na-update Mar 4, 2026 · NCT04639336

Mula sa ClinicalTrials.gov, na-kuha noong Okt 6, 2026. Ang bawat pag-aaral ay may sariling pamantayan sa eligibility; ang koponan ng pag-aaral ang magdedesisyon kung sino ang makakasali.