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Pag-aaral pangklinika para sa Sakit sa Pag-iimbak ng Glycogen Uri II sa Pennsylvania
4 pag-aaral para sa Sakit sa Pag-iimbak ng Glycogen Uri II ang naghahanap ng mga kalahok sa mga site sa Pennsylvania.
Mga Lungsod sa Pennsylvania
Opisyal na teksto ng pag-aaral (English)
A Study to Evaluate Safety, Tolerability, and Efficacy of AB-1009 Gene Therapy (GAA Gene) in Adult Participants With Late-Onset Pompe Disease (PROGRESS-GT LOPD)
- Hospital of the University of Pennsylvania, Philadelphia
- University of Pittsburgh Medical Center (UPMC), Pittsburgh
Nagre-recruitPhase 1/2
Edad 18 hanggang 65 · Lahat ng kasarian · Na-update Hul 20, 2026 · NCT07282847Pompe Disease Registry Protocol
- Penn State Health Milton South Hershey Medical Center- Site Number : 840126, Hershey
- Children's Hospital of Philadelphia HUP Medical Genetics- Site Number : 840089, Philadelphia
- Children's Hospital of Philadelphia- Site Number : 840034, Philadelphia
- at 2 pa
Nagre-recruitObservasyonal na pag-aaral
Lahat ng edad · Lahat ng kasarian · Na-update Hun 23, 2026 · NCT00231400Study of S-606001 as an Add-on to Enzyme Replacement Therapy (ERT) in Participants With Late-onset Pompe Disease (LOPD)
- University of Pennsylvania, Philadelphia
- University of Pittsburgh School of Medicine, Pittsburgh
Nagre-recruitPhase 2
Edad 18 pataas · Lahat ng kasarian · Na-update Hun 23, 2026 · NCT07123155A Global Prospective Observational Registry of Patients With Pompe Disease
- University of Pennsylvania Perelman Center for Advanced Medicine, Philadelphia
- University of Pittsburgh, Pittsburgh
- UPMC Children's Hospital of Pittsburgh, Pittsburgh
Nagre-recruitObservasyonal na pag-aaral
Lahat ng edad · Lahat ng kasarian · Na-update Mar 10, 2026 · NCT06121011Mula sa ClinicalTrials.gov, na-kuha noong Okt 5, 2026. Ang bawat pag-aaral ay may sariling pamantayan sa eligibility; ang koponan ng pag-aaral ang magdedesisyon kung sino ang makakasali.