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Pag-aaral pangklinika para sa Hemophilia B sa California

7 pag-aaral para sa Hemophilia B ang naghahanap ng mga kalahok sa mga site sa California.

Mga Lungsod sa California

Opisyal na teksto ng pag-aaral (English)

Safety and Effectiveness of Giroctocogene Fitelparvovec or Fidanacogene Elaparvovec in Patients With Hemophilia A or B Respectively

  • The Regents of the University of California||UC Davis Health, Rancho Cordova
  • UC Davis Health, Sacramento
  • UC Davis Ambulatory Care Clinic, Sacramento
  • at 3 pa
Nagre-recruitPhase 3
Edad 18 pataas · Kalalakihan · Na-update Okt 2, 2026 · NCT05568719

Phase 3, Open-label, Single-dose Study of CSL222 in Adolescent Male Subjects (≥ 12 to < 18 Years of Age) With Severe or Moderately Severe Hemophilia B

  • Center for Inherited Blood Disorders, Orange
Nagre-recruitPhase 3
138 Months – 206 Months · Kalalakihan · Na-update Set 16, 2026 · NCT07080905

A Study to Investigate the Safety and Effectiveness of a Coagulation Factor IX Gene Insertion Therapy (REGV131-LNP1265) in Pediatric, Adolescent and Adult Participants With Hemophilia B

  • Orthopaedic Hemophilia Treatment Center, Los Angeles
  • David Geffen School of Medicine at UCLA, Los Angeles
  • Children's Hospital Los Angeles, Los Angeles
  • at 2 pa
Nagre-recruitPhase 1/2
Edad 2 pataas · Kalalakihan · Na-update Set 11, 2026 · NCT06379789

Efficacy and Safety of CSL222 (Etranacogene Dezaparvovec) Gene Therapy in Adults With Hemophilia B With Pretreatment Adeno-associated Virus Serotype 5 (AAV5) Neutralizing Antibodies (Nabs)

  • University of California, San Diego (UCSD), San Diego
Nagre-recruitPhase 3
Edad 18 pataas · Lahat ng kasarian · Na-update Ago 27, 2026 · NCT06003387

ATHN Transcends: A Natural History Study of Non-Neoplastic Hematologic Disorders

  • Orthopaedic Institute for Children HTC, Los Angeles
  • Childrens Hospital Los Angeles, Los Angeles
  • UCSF Benioff Children's Hospital Oakland, Oakland
  • at 5 pa
Nagre-recruitObservasyonal na pag-aaral
Lahat ng edad · Lahat ng kasarian · Na-update Ago 17, 2026 · NCT04398628

A Study of Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of SR604 in Two Participants Groups (Part A: Healthy Participants, and Part B: Participants With Hemophilia A or Hemophilia B or Factor VII Deficiency)

  • Children's Hospital Los Angeles, Los Angeles
Nagre-recruitPhase 1Malugod na tinatanggap ang malusog na boluntaryo
Edad 18 hanggang 60 · Lahat ng kasarian · Na-update Hul 2, 2026 · NCT06349473

SEVENFACT® for Bleeding Events in Hemophilia With Inhibitors

  • Orthopaedic Institute for Children, Los Angeles
  • University of California at Davis UC Davis Hemostasis and Thrombosis Center, Sacramento
Nagre-recruitPhase 4
Edad 12 hanggang 100 · Lahat ng kasarian · Na-update Ene 12, 2026 · NCT04647227

Mula sa ClinicalTrials.gov, na-kuha noong Okt 6, 2026. Ang bawat pag-aaral ay may sariling pamantayan sa eligibility; ang koponan ng pag-aaral ang magdedesisyon kung sino ang makakasali.