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Pag-aaral pangklinika para sa Hemophilia sa California

14 pag-aaral para sa Hemophilia ang naghahanap ng mga kalahok sa mga site sa California.

Mga Lungsod sa California

Opisyal na teksto ng pag-aaral (English)

Safety and Effectiveness of Giroctocogene Fitelparvovec or Fidanacogene Elaparvovec in Patients With Hemophilia A or B Respectively

  • The Regents of the University of California||UC Davis Health, Rancho Cordova
  • UC Davis Health, Sacramento
  • UC Davis Ambulatory Care Clinic, Sacramento
  • at 3 pa
Nagre-recruitPhase 3
Edad 18 pataas · Kalalakihan · Na-update Okt 2, 2026 · NCT05568719

A Study to Test a Medicine (Fitusiran) for Preventing Bleeds in People With Severe Hemophilia Who Previously Received Preventive Treatment With Emicizumab

  • Children's Hospital Los Angeles- Site Number : 8400005, Los Angeles
Nagre-recruitPhase 4
Edad 12 pataas · Kalalakihan · Na-update Set 23, 2026 · NCT06145373

A Study to Evaluate the Safety, Tolerability, Pharmacokinetics, Pharmacodynamics, and Efficacy of NXT007 in Persons With Severe or Moderate Hemophilia A

  • UC Davis Cancer Center, Sacramento
Nagre-recruitPhase 1/2
Edad 2 hanggang 59 · Kalalakihan · Na-update Set 11, 2026 · NCT05987449

A Gene Therapy Study of SPK-8011QQ in Adults With Severe or Moderately Severe Hemophilia A

  • Center for Inherited Blood Disorders, Orange
  • University of California San Francisco, San Francisco
  • Kaiser Permanente, Vallejo
Nagre-recruitPhase 1/2
Edad 18 pataas · Kalalakihan · Na-update Set 11, 2026 · NCT07226206

A Clinical Study to Evaluate the Effects of NXT007 Compared to Emicizumab Prophylaxis in People With Hemophilia A

  • Center for Inherited Blood Disorders, Orange
Nagre-recruitPhase 3
Edad 12 pataas · Lahat ng kasarian · Na-update Set 4, 2026 · NCT07416604

Pharmacokinetics, Pharmacodynamics, and Safety Profile of Understudied Drugs Administered to Children Per Standard of Care (POPS)

  • Lucile Packard Children's Hospital, Palo Alto
Nagre-recruitObservasyonal na pag-aaralMalugod na tinatanggap ang malusog na boluntaryo
Edad 0 hanggang 20 · Lahat ng kasarian · Na-update Ago 21, 2026 · NCT04278404

ATHN Transcends: A Natural History Study of Non-Neoplastic Hematologic Disorders

  • Orthopaedic Institute for Children HTC, Los Angeles
  • Childrens Hospital Los Angeles, Los Angeles
  • UCSF Benioff Children's Hospital Oakland, Oakland
  • at 5 pa
Nagre-recruitObservasyonal na pag-aaral
Lahat ng edad · Lahat ng kasarian · Na-update Ago 17, 2026 · NCT04398628

A Study to Investigate the Efficacy and Safety of Fitusiran Prophylaxis in Male Participants Aged 1 to Less Than 12 Years With Hemophilia A or B

  • The Luskin Orthopaedic Institute for Children- Site Number : 8400013, Los Angeles
  • The Center for Inherited Blood Disorders- Site Number : 8400009, Orange
Nagre-recruitPhase 3
Edad 1 hanggang 11 · Kalalakihan · Na-update Ago 17, 2026 · NCT07285460

Prevention of Bleeding in Patients With Moderate and Severe Hemophilia A Playing Sports: A Comparison Between Factor VIII and Emicizumab Prophylaxis

  • Stanford University, Palo Alto
  • Rady Children's Hospital, San Diego
Nagre-recruitObservasyonal na pag-aaral
Edad 6 hanggang 19 · Lahat ng kasarian · Na-update Hul 2, 2026 · NCT05022459

A Study of Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of SR604 in Two Participants Groups (Part A: Healthy Participants, and Part B: Participants With Hemophilia A or Hemophilia B or Factor VII Deficiency)

  • Children's Hospital Los Angeles, Los Angeles
Nagre-recruitPhase 1Malugod na tinatanggap ang malusog na boluntaryo
Edad 18 hanggang 60 · Lahat ng kasarian · Na-update Hul 2, 2026 · NCT06349473

A Study to Learn About How Changing Therapy From Emicizumab to Marstacimab Affects People With the Severe Hemophilia A.

  • Orthopaedic Institute for Children/Orthopaedic Hemophilia Treatment Center, Los Angeles
Nagre-recruitPhase 1
Edad 12 hanggang 74 · Kalalakihan · Na-update Hun 3, 2026 · NCT06703606

Emicizumab for Severe Von Willebrand Disease (VWD) and VWD/Hemophilia A

  • The Center for Comprehensive Care and Diagnosis of Inherited Blood Disorders (CIBD), Orange
  • Stanford University: Stanford Children's Health, Redwood City
Nagre-recruitPhase 1
Edad 0 hanggang 90 · Lahat ng kasarian · Na-update Abr 3, 2026 · NCT05500807

SEVENFACT® for Bleeding Events in Hemophilia With Inhibitors

  • Orthopaedic Institute for Children, Los Angeles
  • University of California at Davis UC Davis Hemostasis and Thrombosis Center, Sacramento
Nagre-recruitPhase 4
Edad 12 hanggang 100 · Lahat ng kasarian · Na-update Ene 12, 2026 · NCT04647227

Efanesoctocog Alfa Prophylaxis in Patients With Hemophilia A With Synovial Hypertrophy

  • Orthopedic Institute for Children- Site Number : 8400009, Los Angeles
Nagre-recruitPhase 4
Edad 12 pataas · Lahat ng kasarian · Na-update Nob 18, 2025 · NCT06941870

Mula sa ClinicalTrials.gov, na-kuha noong Okt 5, 2026. Ang bawat pag-aaral ay may sariling pamantayan sa eligibility; ang koponan ng pag-aaral ang magdedesisyon kung sino ang makakasali.